Clinical variability and genetic homogeneity of the camptodactyly-arthropathy-coxa vara-pericarditis syndrome

Am J Med Genet. 2000 Nov 27;95(3):233-6. doi: 10.1002/1096-8628(20001127)95:3<233::aid-ajmg9>3.0.co;2-3.

Abstract

The camptodactyly-arthropathy-coxa vara-pericarditis syndrome (CACP) is an autosomal recessive condition characterized by the association of congenital or early onset camptodactyly and noninflammatory arthropathy with synovial hyperplasia. Progressive coxa vara deformity and/or noninflammatory pericardial or pleural effusions have been observed in some patients. Recently, the disease gene has been assigned to human chromosome region 1q25-q31, and truncating mutations have been identified in the megakaryocyte stimulating factor gene. Studying 12 patients from 8 unrelated families, we emphasized hip and spine involvement, particularly in the course of the disease as shown in a 58-year-old patient. Despite clinical variability, linkage studies support genetic homogeneity of the disease.

MeSH terms

  • Adolescent
  • Child
  • Child, Preschool
  • Chromosomes, Human, Pair 1
  • Female
  • Genetic Heterogeneity
  • Genetic Linkage
  • Hip
  • Humans
  • Joint Diseases / diagnostic imaging
  • Joint Diseases / genetics*
  • Joint Diseases / pathology*
  • Male
  • Microsatellite Repeats
  • Middle Aged
  • Osteoporosis / genetics
  • Pericarditis / genetics*
  • Pericarditis / pathology
  • Phenotype
  • Radiography
  • Syndrome