Shwachman-Diamond syndrome with exocrine pancreatic dysfunction and bone marrow failure maps to the centromeric region of chromosome 7

Am J Hum Genet. 2001 Apr;68(4):1048-54. doi: 10.1086/319505. Epub 2001 Mar 15.

Abstract

Shwachman-Diamond syndrome (SDS) is an autosomal recessive disorder characterized by exocrine pancreatic insufficiency and hematologic and skeletal abnormalities. A genomewide scan of families with SDS was terminated at approximately 50% completion, with the identification of chromosome 7 markers that showed linkage with the disease. Finer mapping revealed significant linkage across a broad interval that included the centromere. The maximum two-point LOD score was 8.7, with D7S473, at a recombination fraction of 0. The maximum multipoint LOD score was 10, in the interval between D7S499 and D7S482 (5.4 cM on the female map and 0 cM on the male map), a region delimited by recombinant events detected in affected children. Evidence from all 15 of the multiplex families analyzed provided support for the linkage, consistent with a single locus for SDS. However, the presence of several different mutations is suggested by the heterogeneity of disease-associated haplotypes in the candidate region.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Alleles
  • Bone Marrow Diseases / blood
  • Bone Marrow Diseases / genetics*
  • Bone Marrow Diseases / pathology
  • Centromere / genetics*
  • Chromosome Mapping
  • Chromosomes, Human, Pair 7 / genetics*
  • Exocrine Pancreatic Insufficiency / genetics*
  • Exocrine Pancreatic Insufficiency / pathology
  • Female
  • Gene Frequency
  • Genes, Recessive / genetics
  • Genetic Heterogeneity
  • Genetic Linkage / genetics*
  • Haplotypes / genetics
  • Humans
  • Lod Score
  • Male
  • Models, Genetic
  • Musculoskeletal Abnormalities / genetics
  • Musculoskeletal Abnormalities / pathology
  • Mutation / genetics
  • Myeloid Cells / pathology
  • Pedigree
  • Software
  • Syndrome