Enforced expression of GATA-3 severely reduces human thymic cellularity

J Immunol. 2001 Oct 15;167(8):4468-75. doi: 10.4049/jimmunol.167.8.4468.

Abstract

Following bone marrow transplantation, patients often suffer from immune incompetence by reduced or late T cell development. Moreover, adult bone marrow stem cells have a lower capacity to generate T cells compared with fetal liver- and umbilical cord blood-derived progenitors. Therefore, enhancing thymic-dependent T cell generation might hold great therapeutic potential. GATA-3 is a transcription factor that is essential in T cell development. In this study we examined the therapeutic potential of GATA-3 to enhance T cell generation by overexpressing GATA-3 in T cell progenitors followed by fetal thymic organ culture (FTOC). We observed that early during FTOC, there was an enhanced differentiation toward the double positive stage of T cell development. From day 10 of FTOC, however, overexpression of GATA-3 induced a severe reduction in thymic cellularity, which probably correlates with the absence of a functional TCR-beta chain. We further show that the frequency of apoptosis was increased in GATA-3-transduced thymocytes. Despite the absence of a functional TCR-beta chain, GATA-3 transduced progenitors were able to differentiate into CD8beta(+) double positive thymocytes. This study shows that a strictly regulated expression of GATA-3 is essential for normal T cell development and this puts severe restrictions on the potential therapeutic use of continuously overexpressed GATA-3.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Antigens, Differentiation, T-Lymphocyte
  • Apoptosis
  • CD3 Complex
  • CD4 Antigens
  • CD8 Antigens
  • Cell Differentiation
  • Cloning, Molecular
  • DNA-Binding Proteins / biosynthesis*
  • DNA-Binding Proteins / genetics
  • GATA3 Transcription Factor
  • Gene Expression Regulation
  • Gene Transfer Techniques
  • Genes, T-Cell Receptor beta
  • Hematopoietic Stem Cells / cytology*
  • Hematopoietic Stem Cells / immunology
  • Humans
  • Organ Culture Techniques
  • T-Lymphocytes / cytology*
  • T-Lymphocytes / immunology
  • Thymus Gland / cytology*
  • Thymus Gland / immunology
  • Trans-Activators / biosynthesis*
  • Trans-Activators / genetics

Substances

  • Antigens, Differentiation, T-Lymphocyte
  • CD3 Complex
  • CD4 Antigens
  • CD8 Antigens
  • DNA-Binding Proteins
  • GATA3 Transcription Factor
  • GATA3 protein, human
  • Trans-Activators