A novel protocol that allows short-term stem cell expansion of both committed and pluripotent hematopoietic progenitor cells suitable for clinical use

Blood Cells Mol Dis. 2001 Jul-Aug;27(4):715-24; discussion 725-7. doi: 10.1006/bcmd.2001.0439.

Abstract

To obtain long-term engraftment and hematopoiesis in myeloablated patients, the cell population used for hematopoietic reconstitution should include a sufficient number of early pluripotent hematopoietic stem cells (HSCs), along with committed cells from the various lineages. For this purpose, the small subset of CD34+ cells purified from different sources must be expanded ex vivo. Since cytokines may induce both proliferation and differentiation, expansion would provide a cell population comprising committed as well as uncommitted cells. Optimization of HSC expansion methods could be obtained by a combination of cytokines able to sustain renewal of pluripotent cells yet endowed with poor differentiation potential. We used variations of the combinations of cytokines described by Brugger et al. [W. Brugger, S. Heimfels, R. J. Berenson, R. Mertelsmann, and L. Kanz (1995) N. Engl. J. Med. 333, 283-287] and Piacibello et al. [W. Piacibello, F. Sanavio, L. Garetto, A. Severino, D. Bergandi, J. Ferrario, F. Fagioli, M. Berger, and M. Aglietta (1997) Blood 89, 2644-2653] to expand UCB CD34+ cells and monitored proliferation rate and phenotype after 14 days of culture. Several hematopoietic lineage-associated surface antigens were evaluated. Our data show that flt3L and thrombopoietin in combination with IL-3, while sustaining a high CD34+ proliferation rate, provide a relatively low enrichment in very early uncommitted CD34+/CD38- cells. Conversely, in the absence of IL-3, they are less effective in inducing proliferation yet significantly increase the number of CD34+/CD38- cells. A combination of the above protocols, applied simultaneously to aliquots of the same sample, would allow expansion of both committed and pluripotent HSC. This strategy may represent a significant improvement for clinical applications.

Publication types

  • Comparative Study

MeSH terms

  • ADP-ribosyl Cyclase
  • ADP-ribosyl Cyclase 1
  • Antigens, CD*
  • Antigens, CD34 / analysis
  • Antigens, Differentiation / analysis
  • Cell Culture Techniques / methods*
  • Cell Differentiation
  • Cell Division / drug effects
  • Drug Synergism
  • Erythropoietin / pharmacology
  • Fetal Blood / cytology
  • Flow Cytometry
  • Hematopoietic Stem Cell Transplantation / methods*
  • Hematopoietic Stem Cells / classification
  • Hematopoietic Stem Cells / cytology*
  • Hematopoietic Stem Cells / drug effects
  • Humans
  • Immunomagnetic Separation
  • Immunophenotyping
  • Infant, Newborn
  • Interleukin-3 / pharmacology
  • Interleukin-6 / pharmacology
  • Membrane Glycoproteins
  • Membrane Proteins / pharmacology
  • NAD+ Nucleosidase / analysis
  • Stem Cell Factor / pharmacology
  • Thrombopoietin / pharmacology

Substances

  • Antigens, CD
  • Antigens, CD34
  • Antigens, Differentiation
  • Interleukin-3
  • Interleukin-6
  • Membrane Glycoproteins
  • Membrane Proteins
  • Stem Cell Factor
  • flt3 ligand protein
  • Erythropoietin
  • Thrombopoietin
  • ADP-ribosyl Cyclase
  • CD38 protein, human
  • NAD+ Nucleosidase
  • ADP-ribosyl Cyclase 1