A phage display selected fab fragment with MHC class I-restricted specificity for MAGE-A1 allows for retargeting of primary human T lymphocytes

Gene Ther. 2001 Nov;8(21):1601-8. doi: 10.1038/sj.gt.3301570.

Abstract

The clinical benefit of adoptive transfer of MHC-restricted cytotoxic T lymphocytes(CTL) for the treatment of cancer is hampered by the low success rate to generate antitumor CTLs. To bypass the need for tumor-specific CTL, we developed a strategy that allows for grafting of human T lymphocytes with MHC-restricted antigen specificity using in vitro selected human Fab fragments fused to the Fc(epsilon)RI-gamma signaling molecule. Retroviral introduction of a Fab-based chimeric receptor specific for MAGE-A1/HLA-A1 into primary human T lymphocytes resulted in binding of relevant peptide/MHC complexes. Transduced T lymphocytes responded to native MAGE-A1/HLA-A1POS target cells by specific cytokine production and cytolysis. Therefore, peptide/MHC-specific Fab fragments represent new alternatives to TCR to confer human T lymphocytes with tumor specificity, which provides a promising rationale for developing immunogene therapies.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Antigens, Neoplasm
  • Epitopes
  • Genetic Therapy / methods*
  • Genetic Vectors / administration & dosage
  • HLA-A1 Antigen / immunology
  • Humans
  • Immunoglobulin Fab Fragments / genetics*
  • Immunoglobulin Fab Fragments / metabolism
  • Immunotherapy, Adoptive / methods*
  • Melanoma / immunology
  • Melanoma / therapy*
  • Melanoma-Specific Antigens
  • Neoplasm Proteins / immunology
  • Peptide Library
  • Receptors, Immunologic / genetics*
  • Retroviridae / genetics
  • T-Lymphocytes, Cytotoxic / immunology
  • Transduction, Genetic
  • Tumor Cells, Cultured

Substances

  • Antigens, Neoplasm
  • Epitopes
  • HLA-A1 Antigen
  • Immunoglobulin Fab Fragments
  • Melanoma-Specific Antigens
  • Neoplasm Proteins
  • Peptide Library
  • Receptors, Immunologic