Naked DNA injection for liver metastases treatment in rats

Hepatology. 2002 May;35(5):1144-52. doi: 10.1053/jhep.2002.32709.

Abstract

The cytosine deaminase (CD) gene converts the nontoxic prodrug, 5-fluorocytosine (5-FC), into 5-fluorouracil (5-FU). We previously showed that injection of CD-bearing cancer cells followed by 5-FC treatment can act as an autologous tumor vaccine in a syngenic liver metastasis model in rats. In the present work, we analyzed the antitumor efficiency of a direct intratumoral injection of a CD-expressing plasmid. In rats bearing microscopic or macroscopic metastases in right and left liver lobes, an injection of a CD-expressing plasmid was performed in the left lobe tumor, followed by 5-FC treatment of the animals. A significant regression of the DNA-injected tumor was observed in 5-FC-treated rats, both in microscopic (P =.007) or advanced (P <.0001) tumor models. Moreover, this treatment also induced a potent distant bystander effect on untreated controlateral liver tumors and extrahepatic metastases, resulting in an increased survival compared with control animals in both tumor models (P <.05). In conclusion, these data suggest that direct intratumoral injection of a CD-expressing plasmid, associated to 5-FC administration, can constitute a powerful and innocuous alternative treatment for unresectable liver metastases from colon carcinoma.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antimetabolites / pharmacokinetics
  • Colonic Neoplasms
  • Cytosine Deaminase
  • Disease Models, Animal
  • Flucytosine / pharmacokinetics
  • Fluorouracil / metabolism
  • Gene Transfer Techniques
  • Genetic Therapy*
  • Hepatectomy
  • Killer Cells, Natural / immunology
  • Liver Neoplasms, Experimental / mortality
  • Liver Neoplasms, Experimental / secondary*
  • Liver Neoplasms, Experimental / therapy*
  • Male
  • Neoplasm Transplantation
  • Nucleoside Deaminases / genetics*
  • Plasmids / pharmacology*
  • Rats
  • Rats, Inbred Strains
  • Survival Rate
  • Tumor Cells, Cultured / transplantation

Substances

  • Antimetabolites
  • Flucytosine
  • Nucleoside Deaminases
  • Cytosine Deaminase
  • Fluorouracil