Identification of novel sequence variants in the neurofilament-light gene in a Japanese population: analysis of Charcot-Marie-Tooth disease patients and normal individuals

J Peripher Nerv Syst. 2002 Dec;7(4):221-4. doi: 10.1046/j.1529-8027.2002.02028.x.

Abstract

Mutations of the neurofilament-light (NEFL/NF-L) gene were examined in 124 unrelated Japanese patients with Charcot-Marie-Tooth disease (CMT) without known gene mutations, and 248 normal Japanese individuals. A new method, which can detect basepair mismatches with RNase cleavage on agarose gel electrophoresis, coupled with DNA sequencing, identified 8 novel sequence variations in the NF-L gene. In these sequence variants, 5 variants were polymorphisms, including 3 single nucleotide polymorphisms (SNPs), and 3 other missense mutations (Pro22Thr, Asn97Ser and Ala148Val) were found in the patients with CMT phenotype. The variant alleles in the NF-L gene could influence the developing process of CMT phenotype and also might cause CMT phenotype.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Amino Acid Substitution / genetics
  • Charcot-Marie-Tooth Disease / genetics*
  • Genetic Variation / genetics*
  • Humans
  • Japan
  • Male
  • Middle Aged
  • Mutation / genetics
  • Neurofilament Proteins / genetics*
  • Polymorphism, Genetic / genetics

Substances

  • Neurofilament Proteins
  • neurofilament protein L