A new xenograft model for graft-versus-host disease by intravenous transfer of human peripheral blood mononuclear cells in RAG2-/- gammac-/- double-mutant mice

Blood. 2003 Oct 1;102(7):2522-31. doi: 10.1182/blood-2002-10-3241. Epub 2003 Jun 5.

Abstract

The safe application of new strategies for the treatment of graft-versus-host disease (GVHD) is hampered by the lack of a clinically relevant model for preclinical testing. Current models are based on intraperitoneal transfer of human peripheral blood mononuclear cells (huPBMCs) into NOD-SCID (nonobese diabetic-severe combined immunodeficient)/SCID mice. Intravenous transfer would be preferred but this has always been ineffective. We developed a new model for xenogeneic GVHD (X-GVHD) by intravenous transfer of huPBMCs into RAG2-/- gammac-/-mice. Our results show a high human T-cell chimerism of more than 20% (up to 98%) in more than 90% of mice, associated with a consistent development of XGVHD within 14 to 28 days and a total mortality rate of 85% shorter than 2 months. After murine macrophage depletion, engraftment was earlier and equally high with lower doses of huPBMCs. Human macrophages were also absent in these mice. Purified huCD3+ cells showed a similar X-GVH effect with contribution of both CD4 and CD8 phenotypes. Human immunoglobulins and cytokines were produced in diseased mice. One of 30 mice developed chronic X-GVHD with skin histology similar to human GVHD. In conclusion, we present a new model for X-GVHD by intravenous transfer of huPBMCs in RAG2-/- gammac-/- mice. Murine and human macrophages do not seem to be necessary for acute X-GVHD in this model.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antimetabolites / pharmacology
  • CD4-CD8 Ratio
  • Clodronic Acid / pharmacology
  • Cytokines / blood
  • DNA-Binding Proteins / genetics*
  • Disease Models, Animal*
  • Female
  • Gene Rearrangement, T-Lymphocyte / genetics
  • Graft vs Host Disease / immunology*
  • Graft vs Host Disease / physiopathology
  • Humans
  • Immunoglobulin G / blood
  • Immunoglobulin M / blood
  • Injections, Intravenous
  • Kidney / cytology
  • Leukocytes, Mononuclear / transplantation*
  • Liver / cytology
  • Lung / cytology
  • Macrophages / cytology
  • Macrophages / drug effects
  • Male
  • Mice
  • Mice, Mutant Strains*
  • Nuclear Proteins
  • Phenotype
  • Skin / cytology
  • Spleen / cytology
  • T-Lymphocytes / physiology
  • Titrimetry
  • Transplantation Chimera
  • Transplantation, Heterologous*
  • Transplants

Substances

  • Antimetabolites
  • Cytokines
  • DNA-Binding Proteins
  • Immunoglobulin G
  • Immunoglobulin M
  • Nuclear Proteins
  • RAG2 protein, human
  • Rag2 protein, mouse
  • V(D)J recombination activating protein 2
  • Clodronic Acid