Reduced-intensity preparative regimen and allogeneic stem cell transplantation for advanced solid tumors

Blood. 2004 Jan 15;103(2):435-41. doi: 10.1182/blood-2003-07-2236. Epub 2003 Aug 28.

Abstract

In this prospective multicenter program, we investigated allogeneic stem cell transplantation (ASCT) from HLA-identical siblings following reduced-intensity conditioning (RIC) regimen for patients with refractory metastatic solid tumors (STs). Fifty-seven patients, of whom 39 had a progressive disease (PD) at time of ASCT, received an RIC ASCT combining fludarabine, antithymocyte globulin (ATG), and busulfan. Patients were analyzed in terms of engraftment, transplant-related mortality (TRM), disease response, and outcome. In this setting, RIC was associated with rapid engraftment and low overall TRM (9% [95% confidence interval (CI), 1%-16%]). The cumulative incidence of objective responses (ORs) reached 14% (95% CI, 6%-30%) with this being significantly higher in patients without PD (44% [95% CI, 21%-67%] versus 0; P <.0001) at time of ASCT. Achievement of OR translated into a significantly better overall survival (OS). In multivariate analysis, OS was significantly influenced by disease status at time of ASCT (odds ratio, 4.88; P <.001) and chronic graft-versus-host disease (GVHD) occurrence (odds ratio, 2.86; P <.01). Overall, these results showed that OR can occur after RIC ASCT for resistant ST with a relatively low TRM and potential benefit especially in patients with slowly progressive disease. Further studies are warranted in patients with less advanced ST.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Acute Disease
  • Adult
  • Antilymphocyte Serum / therapeutic use
  • Bone Marrow Transplantation / mortality
  • Busulfan / therapeutic use
  • Chronic Disease
  • Disease Progression
  • Female
  • Graft vs Host Disease / epidemiology
  • Humans
  • Immunosuppressive Agents / therapeutic use
  • Male
  • Middle Aged
  • Neoplasm Metastasis
  • Neoplasms / classification
  • Neoplasms / pathology
  • Neoplasms / surgery
  • Neoplasms / therapy*
  • Siblings
  • Stem Cell Transplantation* / mortality
  • Survival Analysis
  • Tissue Donors
  • Transplantation Conditioning / methods*
  • Transplantation, Homologous
  • Treatment Outcome
  • Vidarabine / analogs & derivatives*
  • Vidarabine / therapeutic use

Substances

  • Antilymphocyte Serum
  • Immunosuppressive Agents
  • Vidarabine
  • Busulfan
  • fludarabine