Myosin storage myopathy associated with a heterozygous missense mutation in MYH7

Ann Neurol. 2003 Oct;54(4):494-500. doi: 10.1002/ana.10693.

Abstract

Myosin constitutes the major part of the thick filaments in the contractile apparatus of striated muscle. MYH7 encodes the slow/beta-cardiac myosin heavy chain (MyHC), which is the main MyHC isoform in slow, oxidative, type 1 muscle fibers of skeletal muscle. It is also the major MyHC isoform of cardiac ventricles. Numerous missense mutations in the globular head of slow/beta-cardiac MyHC are associated with familial hypertrophic cardiomyopathy. We identified a missense mutation, Arg1845Trp, in the rod region of slow/beta-cardiac MyHC in patients with a skeletal myopathy from two different families. The myopathy was characterized by muscle weakness and wasting with onset in childhood and slow progression, but no overt cardiomyopathy. Slow, oxidative, type 1 muscle fibers showed large inclusions consisting of slow/beta-cardiac MyHC. The features were similar to a previously described entity: hyaline body myopathy. Our findings indicate that the mutated residue of slow/beta-cardiac MyHC is essential for the assembly of thick filaments in skeletal muscle. We propose the term myosin storage myopathy for this disease.

Publication types

  • Comparative Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adenosine Triphosphatases / metabolism
  • Aged
  • Arginine / genetics
  • Blotting, Western
  • DNA Mutational Analysis
  • Family Health
  • Female
  • Heterozygote*
  • Humans
  • Immunohistochemistry
  • Male
  • Microscopy, Electron
  • Molecular Motor Proteins*
  • Molecular Sequence Data
  • Muscle Fibers, Slow-Twitch / metabolism
  • Muscle Fibers, Slow-Twitch / ultrastructure
  • Muscular Diseases / genetics*
  • Muscular Diseases / metabolism
  • Muscular Diseases / pathology
  • Mutation, Missense*
  • Myosin Heavy Chains / genetics*
  • Myosin Heavy Chains / metabolism
  • Myosin Heavy Chains / ultrastructure
  • Protein Isoforms
  • Sequence Alignment
  • Staining and Labeling
  • Tryptophan / genetics

Substances

  • MYH9 protein, human
  • Molecular Motor Proteins
  • Protein Isoforms
  • Tryptophan
  • Arginine
  • Adenosine Triphosphatases
  • Myosin Heavy Chains