Blockage of VEGF-induced angiogenesis by preventing VEGF secretion

Circ Res. 2004 Jun 11;94(11):1443-50. doi: 10.1161/01.RES.0000129194.61747.bf.

Abstract

Vascular endothelial growth factor (VEGF)/vascular permeability factor is one of the most frequently expressed angiogenic factors in several pathological tissues. Development of VEGF antagonists has become an important approach in the treatment of angiogenesis-dependent diseases. Here we describe a novel anti-VEGF strategy by preventing the secretion of VEGF. We utilize the fact that placenta growth factor (PlGF)-1, a member of the VEGF family lacking detectable angiogenic activity, preferentially forms intracellular heterodimers with VEGF in cells coexpressing both factors. We constructed a retroviral vector containing human PlGF-1 or VEGF with a C-terminal KDEL sequence, which is a mammalian retention signal for the endoplasmic reticulum. Transduction of murine Lewis lung carcinoma cells with the retro-hPlGF-1-KDEL construct almost completely abrogated tumor growth. Consistent with the dramatic antitumor effect, most mouse VEGF molecules remained as intracellular mVEGF/hPlGF-1 heterodimers, and only a negligible amount of mVEGF homodimers were secreted. As a result, in hPlGF-1-KDEL-expressing tumors, blood vessels remained at very low numbers and lacked branching and capillary networks. Gene transfer of a hVEGF-KDEL construct into tumor cells likewise produced a dramatic antitumor effect. Thus, our study provides a novel antiangiogenic approach by preventing the secretion of VEGF.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Angiogenesis Inhibitors / genetics
  • Angiogenesis Inhibitors / therapeutic use*
  • Animals
  • Apoptosis
  • Biological Assay
  • Carcinoma, Lewis Lung / blood supply*
  • Chemotaxis / drug effects
  • Dimerization
  • Endoplasmic Reticulum / metabolism
  • Endothelial Cells / metabolism
  • Female
  • Genetic Therapy*
  • Genetic Vectors / genetics
  • Genetic Vectors / therapeutic use
  • Humans
  • Mice
  • Mice, Inbred C57BL
  • Neoplasm Transplantation
  • Neovascularization, Pathologic / drug therapy*
  • Oligopeptides / genetics
  • Placenta Growth Factor
  • Pregnancy Proteins / genetics
  • Pregnancy Proteins / physiology*
  • Protein Sorting Signals / genetics
  • Recombinant Fusion Proteins / chemistry
  • Recombinant Fusion Proteins / physiology
  • Retroviridae / genetics
  • Sus scrofa
  • Transduction, Genetic
  • Vascular Endothelial Growth Factor A / chemistry
  • Vascular Endothelial Growth Factor A / metabolism*
  • Vascular Endothelial Growth Factor Receptor-1 / metabolism
  • Vascular Endothelial Growth Factor Receptor-2 / metabolism

Substances

  • Angiogenesis Inhibitors
  • Oligopeptides
  • PGF protein, human
  • Pgf protein, mouse
  • Pregnancy Proteins
  • Protein Sorting Signals
  • Recombinant Fusion Proteins
  • VEGFA protein, human
  • Vascular Endothelial Growth Factor A
  • lysyl-aspartyl-glutamyl-leucine
  • Placenta Growth Factor
  • Vascular Endothelial Growth Factor Receptor-1
  • Vascular Endothelial Growth Factor Receptor-2