Hypoxia-regulated therapeutic gene as a preemptive treatment strategy against ischemia/reperfusion tissue injury

Proc Natl Acad Sci U S A. 2004 Aug 17;101(33):12282-7. doi: 10.1073/pnas.0404616101. Epub 2004 Aug 9.

Abstract

Ischemia and reperfusion represent major mechanisms of tissue injury and organ failure. The timing of administration and the duration of action limit current treatment approaches using pharmacological agents. In this study, we have successfully developed a preemptive strategy for tissue protection using an adenoassociated vector system containing erythropoietin hypoxia response elements for ischemia-regulated expression of the therapeutic gene human heme-oxygenase-1 (hHO-1). We demonstrate that a single administration of this vector several weeks in advance of ischemia/reperfusion injury to multiple tissues such as heart, liver, and skeletal muscle yields rapid and timely induction of hHO-1 during ischemia that resulted in dramatic reduction in tissue damage. In addition, overexpression of therapeutic transgene prevented long-term pathological tissue remodeling and normalized tissue function. Application of this regulatable system using an endogenous physiological stimulus for expression of a therapeutic gene may be a feasible strategy for protecting tissues at risk of ischemia/reperfusion injury.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Animals
  • Cell Line
  • Cytokines / genetics
  • Gene Expression Regulation
  • Genetic Therapy / methods*
  • Green Fluorescent Proteins
  • Heme Oxygenase (Decyclizing) / genetics*
  • Heme Oxygenase-1
  • Humans
  • Hypoxia / genetics*
  • Liver / enzymology
  • Liver / immunology
  • Luciferases / biosynthesis
  • Luciferases / genetics
  • Luminescent Proteins / biosynthesis
  • Luminescent Proteins / genetics
  • Male
  • Membrane Proteins
  • Muscle, Skeletal / enzymology
  • Muscle, Skeletal / injuries
  • Myocardial Reperfusion Injury / enzymology
  • Myocardial Reperfusion Injury / genetics
  • Myocardial Reperfusion Injury / therapy
  • Rats
  • Rats, Sprague-Dawley
  • Recombinant Proteins / biosynthesis
  • Recombinant Proteins / genetics
  • Reperfusion Injury / enzymology
  • Reperfusion Injury / genetics
  • Reperfusion Injury / therapy*

Substances

  • Cytokines
  • Luminescent Proteins
  • Membrane Proteins
  • Recombinant Proteins
  • Green Fluorescent Proteins
  • Luciferases
  • HMOX1 protein, human
  • Heme Oxygenase (Decyclizing)
  • Heme Oxygenase-1