CXCR4-transgene expression significantly improves marrow engraftment of cultured hematopoietic stem cells

Stem Cells. 2004;22(7):1128-33. doi: 10.1634/stemcells.2003-0196.

Abstract

Hematopoietic stem cells (HSCs) lose marrow reconstitution potential during ex vivo culture. HSC migration to stromal cell-derived factor (SDF)-1 (CXCL12) correlates with CXC chemokine receptor 4 (CXCR4) expression and marrow engraftment. We demonstrate that mobilized human CD34+ peripheral blood stem cells (CD34+ PBSCs) lose CXCR4 expression during prolonged culture. We transduced CD34+ PBSCs with retrovirus vector encoding human CXCR4 and achieved 18-fold more CXCR4 expression in over 87% of CD34+ cells. CXCR4-transduced cells yielded increased calcium flux and up to a 10-fold increase in migration to SDF-1. Six-day cultured CXCR4-transduced cells demonstrated significant engraftment in nonobese diabetic/severe combined immunodeficient mice under conditions in which control transduced cells resulted in low or no engraftment. We conclude that transduction-mediated overexpression of CXCR4 significantly improves marrow engraftment of cultured PBSCs.

MeSH terms

  • Animals
  • Antigens, CD34 / biosynthesis
  • Bone Marrow Cells / cytology*
  • Calcium / metabolism
  • Cell Movement
  • Flow Cytometry
  • Gene Transfer Techniques*
  • Graft Survival
  • Hematopoietic Stem Cell Transplantation / methods*
  • Hematopoietic Stem Cells / cytology*
  • Humans
  • Membrane Glycoproteins / metabolism
  • Mice
  • Mice, SCID
  • NADPH Oxidase 2
  • NADPH Oxidases / metabolism
  • Receptors, CXCR4 / biosynthesis*
  • Receptors, CXCR4 / genetics*
  • Signal Transduction
  • Time Factors
  • Transgenes*

Substances

  • Antigens, CD34
  • Membrane Glycoproteins
  • Receptors, CXCR4
  • CYBB protein, human
  • NADPH Oxidase 2
  • NADPH Oxidases
  • Calcium