Identification of small-molecule antagonists that inhibit an activator: coactivator interaction

Proc Natl Acad Sci U S A. 2004 Dec 21;101(51):17622-7. doi: 10.1073/pnas.0406374101. Epub 2004 Dec 7.

Abstract

Phosphorylation of the cAMP response element binding protein (CREB) at Ser-133 in response to hormonal stimuli triggers cellular gene expression via the recruitment of the histone acetylase coactivator paralogs CREB binding protein (CBP) and p300 to the promoter. The NMR structure of the CREB:CBP complex, using relevant interaction domains called KID and KIX, respectively, reveals a shallow hydrophobic groove on the surface of KIX that accommodates an amphipathic helix in phospho (Ser-133) KID. Using an NMR-based screening approach on a preselected small-molecule library, we identified several compounds that bind to different surfaces on KIX. One of these, KG-501 (2-naphthol-AS-E-phosphate), targeted a surface distal to the CREB binding groove that includes Arg-600, a residue that is required for the CREB:CBP interaction. When added to live cells, KG-501 disrupted the CREB: CBP complex and attenuated target gene induction in response to cAMP agonist. These results demonstrate the ability of small molecules to interfere with second-messenger signaling cascades by inhibiting specific protein-protein interactions in the nucleus.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • CREB-Binding Protein
  • Cell Line
  • Cyclic AMP Response Element-Binding Protein / antagonists & inhibitors*
  • Cyclic AMP Response Element-Binding Protein / chemistry
  • Cyclic AMP Response Element-Binding Protein / metabolism*
  • Humans
  • Models, Molecular
  • Naphthols / chemistry
  • Naphthols / pharmacology*
  • Nuclear Magnetic Resonance, Biomolecular
  • Nuclear Proteins / antagonists & inhibitors*
  • Nuclear Proteins / chemistry
  • Nuclear Proteins / metabolism*
  • Organophosphates / chemistry
  • Organophosphates / pharmacology*
  • Phosphoserine / metabolism
  • Protein Binding / drug effects
  • Protein Conformation
  • Signal Transduction / drug effects
  • Trans-Activators / antagonists & inhibitors*
  • Trans-Activators / chemistry
  • Trans-Activators / metabolism*

Substances

  • Cyclic AMP Response Element-Binding Protein
  • Naphthols
  • Nuclear Proteins
  • Organophosphates
  • Trans-Activators
  • naphthol AS-E phosphate
  • Phosphoserine
  • pamoic acid
  • CREB-Binding Protein
  • CREBBP protein, human