Paternal isodisomy for chromosome 2 as the cause of Crigler-Najjar type I syndrome

Eur J Hum Genet. 2005 Mar;13(3):278-82. doi: 10.1038/sj.ejhg.5201342.

Abstract

Crigler-Najjar syndrome type I (CN-I) is a rare and severe autosomal recessive metabolic disease due to a total deficiency of bilirubin uridine diphosphate glucuronosyltransferase located on chromosome 2. We report on a child with CN-I due to a phenylalanine residue deletion inherited only from the father carrying this deletion at the heterozygous state. Cytogenetic analyses showed no deletion of the chromosomal 2q37 region. Microsatellite analysis of the child and his parents was consistent with paternal isodisomy for chromosome 2 in the child. This report demonstrates that uniparental disomy may be at the origin of very rare diseases transmitted as autosomal recessive traits and emphasizes the need for parental DNA analysis in such cases.

Publication types

  • Case Reports

MeSH terms

  • Base Sequence
  • Bilirubin / metabolism
  • Chromosome Mapping
  • Chromosomes, Human, Pair 2*
  • Crigler-Najjar Syndrome / genetics*
  • DNA / analysis
  • Fatal Outcome
  • Fathers
  • Glucuronosyltransferase / deficiency
  • Humans
  • Infant
  • Infant, Newborn
  • Male
  • Microsatellite Repeats
  • Mothers
  • Phenylalanine / analysis
  • Sequence Deletion
  • Uniparental Disomy*

Substances

  • Phenylalanine
  • DNA
  • Glucuronosyltransferase
  • Bilirubin