Lipid emulsions potently increase transgene expression in hepatocytes after adenoviral transfer

Mol Ther. 2006 Jan;13(1):98-107. doi: 10.1016/j.ymthe.2005.06.477. Epub 2005 Aug 19.

Abstract

Elimination of Kupffer cells by cytotoxic clodronate liposomes increases transgene expression in the liver after adenoviral transfer. Here, we demonstrate that empty l-alpha-phosphatidylcholine liposomes block uptake of vectors in the reticuloendothelial cells of the liver and increase human apolipoprotein (apo) A-I (approved gene symbol apo A-I) expression in C57BL/6 (1.3-fold) and Balb/c mice (3.1-fold) to the same extent as clodronate liposomes (1.5- and 3.4-fold, respectively). A similar elevation of human apo A-I levels was induced by the lipid emulsion Intralipid (1.5- and 2.8-fold in C57BL/6 and Balb/c mice, respectively). Not only Kupffer cells but also hepatic sinusoidal endothelial cells (HSEC) constitute the reticuloendothelial cells of the liver. The uptake of adenoviral vectors 1 h after transfer in C57BL/6 mice was 2.9-fold lower in Kupffer cells than in HSEC. In contrast, Kupffer cell uptake in Balb/c mice was 2.6-fold higher than in HSEC. Vector uptake in reticuloendothelial cells of the liver was reduced and transgene expression was increased in splenectomized and Rag2-deficient Balb/c mice but not in splenectomized and Rag1-deficient C57BL/6 mice. In conclusion, lipid emulsions for parenteral clinical use block uptake of adenoviral vectors by the reticuloendothelial cells of the liver and potently increase transgene expression.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adenoviridae / genetics*
  • Animals
  • Apolipoprotein A-I / biosynthesis*
  • Apolipoprotein A-I / genetics
  • Clodronic Acid / chemistry
  • Clodronic Acid / pharmacology*
  • DNA-Binding Proteins / genetics
  • DNA-Binding Proteins / metabolism
  • Fat Emulsions, Intravenous / chemistry
  • Fat Emulsions, Intravenous / pharmacology*
  • Gene Expression
  • Gene Transfer Techniques*
  • Genetic Vectors
  • Hepatocytes / metabolism*
  • Homeodomain Proteins / genetics
  • Homeodomain Proteins / metabolism
  • Humans
  • In Vitro Techniques
  • Kupffer Cells / drug effects
  • Kupffer Cells / metabolism
  • Liposomes
  • Liver / metabolism
  • Mice
  • Mice, Inbred BALB C
  • Mice, Inbred C57BL
  • Phosphatidylcholines / chemistry
  • Phosphatidylcholines / pharmacology*
  • Splenectomy
  • Transduction, Genetic
  • Transgenes

Substances

  • Apolipoprotein A-I
  • DNA-Binding Proteins
  • Fat Emulsions, Intravenous
  • Homeodomain Proteins
  • Liposomes
  • Phosphatidylcholines
  • Rag2 protein, mouse
  • Clodronic Acid
  • RAG-1 protein