Novel recombinant adenoviral vector that targets the interleukin-13 receptor alpha2 chain permits effective gene transfer to malignant glioma

Hum Gene Ther. 2007 Feb;18(2):118-29. doi: 10.1089/hum.2006.146.

Abstract

Transduction of malignant glioma with adenovirus serotype 5 (Ad5) vectors is limited by the low levels of coxsackievirus and adenovirus receptor (CAR) on tumor cells. However, malignant brain tumors have been found to overexpress a glioma-associated receptor, interleukin-13 receptor alpha2 chain (IL-13Ralpha2), a marker of both glial transformation and tumor grade. To selectively target Ad5 to IL-13Ralpha2, we constructed a replication-deficient adenoviral vector that possesses an IL-13 ligand presented by a T4 phage fibritin shaft, and designated the new virus LU-13. Western blot and sequence analyses confirmed proper trimerization and ligand presentation by the T4 fibritin shaft. Confocal microscopy analysis of primary glioma suspensions incubated with viral recombinants showed that LU-13 colocalized with IL-13Ralpha2. Luciferase transduction assays conducted in both primary and passaged glioma cell cultures exhibited at least 10-fold enhanced gene transduction. Moreover, the virus preferentially bound to glioma cells, as documented by increased adenoviral E4 DNA copy number. In vitro competition assays performed with anti-human IL-13 monoclonal antibody confirmed significant attenuation of LU-13 transduction. These results were further confirmed in vivo, where LU-13 showed a 300-fold increase in transgene expression. In summary, we describe here the development of a novel and targeted adenoviral vector that binds IL-13Ralpha2. Our findings confirm the ability of LU-13 to bind IL-13Ralpha2 and increase transgene expression, making it an attractive gene therapy vector for the treatment of malignant glioma in a clinical setting.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adenoviridae / genetics
  • Adenoviridae / metabolism*
  • Animals
  • DNA, Recombinant / genetics
  • DNA, Recombinant / metabolism*
  • Genetic Engineering
  • Genetic Therapy / methods*
  • Genetic Vectors / genetics*
  • Glioma / genetics*
  • Glioma / metabolism
  • Glioma / therapy*
  • Humans
  • Interleukin-13 / metabolism
  • Interleukin-13 Receptor alpha2 Subunit / metabolism*
  • Male
  • Mice
  • Mice, Nude
  • Microscopy, Confocal
  • Reproducibility of Results
  • Transduction, Genetic
  • Transgenes
  • Viral Proteins / metabolism
  • Virus Replication
  • Xenograft Model Antitumor Assays

Substances

  • DNA, Recombinant
  • Interleukin-13
  • Interleukin-13 Receptor alpha2 Subunit
  • Viral Proteins
  • fibritin protein, Enterobacteria phage T4