Design, synthesis, and evaluation of in vivo potency and selectivity of epoxysuccinyl-based inhibitors of papain-family cysteine proteases

Chem Biol. 2007 May;14(5):499-511. doi: 10.1016/j.chembiol.2007.03.010.

Abstract

The papain-family cathepsins are cysteine proteases that are emerging as promising therapeutic targets for a number of human disease conditions ranging from osteoporosis to cancer. Relatively few selective inhibitors for this family exist, and the in vivo selectivity of most existing compounds is unclear. We present here the synthesis of focused libraries of epoxysuccinyl-based inhibitors and their screening in crude tissue extracts. We identified a number of potent inhibitors that display selectivity for endogenous cathepsin targets both in vitro and in vivo. Importantly, the selectivity patterns observed in crude extracts were generally retained in vivo, as assessed by active-site labeling of tissues from treated animals. Overall, this study identifies several important compound classes and highlights the use of activity-based probes to assess pharmacodynamic properties of small-molecule inhibitors in vivo.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Chromatography, High Pressure Liquid
  • Cysteine Proteinase Inhibitors / chemical synthesis*
  • Cysteine Proteinase Inhibitors / pharmacokinetics
  • Cysteine Proteinase Inhibitors / pharmacology*
  • Drug Design
  • Drug Evaluation, Preclinical
  • Epoxy Compounds / chemical synthesis*
  • Epoxy Compounds / pharmacokinetics
  • Epoxy Compounds / pharmacology*
  • Indicators and Reagents
  • Injections, Intraperitoneal
  • Intubation, Gastrointestinal
  • Male
  • Mass Spectrometry
  • Mice
  • Papain / antagonists & inhibitors*
  • Peptide Library
  • Proteomics
  • Rats

Substances

  • Cysteine Proteinase Inhibitors
  • Epoxy Compounds
  • Indicators and Reagents
  • Peptide Library
  • Papain