The chemotherapeutic agent DMXAA potently and specifically activates the TBK1-IRF-3 signaling axis

J Exp Med. 2007 Jul 9;204(7):1559-69. doi: 10.1084/jem.20061845. Epub 2007 Jun 11.

Abstract

Vascular disrupting agents (VDAs) represent a novel approach to the treatment of cancer, resulting in the collapse of tumor vasculature and tumor death. 5,6-dimethylxanthenone-4-acetic acid (DMXAA) is a VDA currently in advanced phase II clinical trials, yet its precise mechanism of action is unknown despite extensive preclinical and clinical investigations. Our data demonstrate that DMXAA is a novel and specific activator of the TANK-binding kinase 1 (TBK1)-interferon (IFN) regulatory factor 3 (IRF-3) signaling pathway. DMXAA treatment of primary mouse macrophages resulted in robust IRF-3 activation and approximately 750-fold increase in IFN-beta mRNA, and in contrast to the potent Toll-like receptor 4 (TLR4) agonist lipopolysaccharide (LPS), signaling was independent of mitogen-activated protein kinase (MAPK) activation and elicited minimal nuclear factor kappaB-dependent gene expression. DMXAA-induced signaling was critically dependent on the IRF-3 kinase, TBK1, and IRF-3 but was myeloid differentiation factor 88-, Toll-interleukin 1 receptor domain-containing adaptor inducing IFN-beta-, IFN promoter-stimulator 1-, and inhibitor of kappaB kinase-independent, thus excluding all known TLRs and cytosolic helicase receptors. DMXAA pretreatment of mouse macrophages induced a state of tolerance to LPS and vice versa. In contrast to LPS stimulation, DMXAA-induced IRF-3 dimerization and IFN-beta expression were inhibited by salicylic acid. These findings detail a novel pathway for TBK1-mediated IRF-3 activation and provide new insights into the mechanism of this new class of chemotherapeutic drugs.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antineoplastic Agents / therapeutic use
  • Cells, Cultured
  • Cytokines / analysis
  • DNA / genetics
  • Enhancer Elements, Genetic
  • Female
  • Gene Expression Regulation / drug effects
  • Immunoglobulin Light Chains / genetics
  • Interferon Regulatory Factor-3 / metabolism*
  • Macrophages, Peritoneal / drug effects
  • Macrophages, Peritoneal / physiology
  • Mice
  • Mice, Inbred C57BL
  • Polymerase Chain Reaction
  • Protein Kinases / metabolism
  • Protein Serine-Threonine Kinases / metabolism*
  • Signal Transduction / drug effects
  • Xanthones / therapeutic use*

Substances

  • Antineoplastic Agents
  • Cytokines
  • Immunoglobulin Light Chains
  • Interferon Regulatory Factor-3
  • Xanthones
  • vadimezan
  • DNA
  • Protein Kinases
  • Tbk1 protein, mouse
  • Protein Serine-Threonine Kinases