Differentiating Alzheimer disease-associated aggregates with small molecules

Neurobiol Dis. 2007 Dec;28(3):251-60. doi: 10.1016/j.nbd.2007.07.018. Epub 2007 Jul 28.

Abstract

Alzheimer disease is diagnosed postmortem by the density and spatial distribution of beta-amyloid plaques and tau-bearing neurofibrillary tangles. The major protein component of each lesion adopts cross-beta-sheet conformation capable of binding small molecules with submicromolar affinity. In many cases, however, Alzheimer pathology overlaps with Lewy body disease, characterized by the accumulation of a third cross-beta-sheet forming protein, alpha-synuclein. To determine the feasibility of distinguishing tau aggregates from beta-amyloid and alpha-synuclein aggregates with small molecule probes, a library containing 72,455 small molecules was screened for antagonists of tau-aggregate-mediated changes in Thioflavin S fluorescence, followed by secondary screens to distinguish the relative affinity for each substrate protein. Results showed that >10-fold binding selectivity among substrates could be achieved, with molecules selective for tau aggregates containing at least three aromatic or rigid moieties connected by two rotatable bonds.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, N.I.H., Intramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Alzheimer Disease / diagnosis*
  • Alzheimer Disease / metabolism*
  • Amyloid beta-Peptides / metabolism
  • Benzothiazoles
  • Dose-Response Relationship, Drug
  • Fluorescent Dyes / chemistry
  • Fluorescent Dyes / pharmacokinetics
  • Humans
  • Mass Spectrometry / methods
  • Neurofibrillary Tangles / metabolism*
  • Peptide Library
  • Plaque, Amyloid / metabolism*
  • Thiazines / chemistry
  • Thiazines / pharmacokinetics
  • Thiazoles / chemistry
  • Thiazoles / pharmacokinetics
  • alpha-Synuclein / metabolism
  • tau Proteins / metabolism

Substances

  • Amyloid beta-Peptides
  • Benzothiazoles
  • Fluorescent Dyes
  • Peptide Library
  • Thiazines
  • Thiazoles
  • alpha-Synuclein
  • tau Proteins
  • thioflavin T