A rapid and quantitative assay for measuring neighboring gene activation by vector proviruses

Mol Ther. 2008 Mar;16(3):534-40. doi: 10.1038/sj.mt.6300398. Epub 2008 Jan 22.

Abstract

A simple, quantitative assay for measuring the oncogenic potential of integrating vectors is needed in order to improve vector design and safety. In this study, we have developed a transient plasmid-based assay to measure the activation of a reporter gene by an adjacent vector provirus. Plasmid pACT contains a luciferase cassette driven by a minimal, enhancerless promoter, into which vector proviruses are inserted upstream for evaluation by luciferase assays and northern blots. In a comparison of analogous vectors based on murine leukemia virus (MLV), human immunodeficiency virus (HIV), and foamy virus (FV), we observed significant enhancer activity and read-through transcription from MLV proviruses, and significant read-through transcription from HIV proviruses. HIV and FV proviruses containing an internal MLV long-terminal repeat (LTR) promoter also had significant enhancer activity, which was not observed with an internal promoter from the murine phosphoglycerate kinase-1 gene, PGK. These results demonstrate that neighboring gene activation can be limited by using internal promoter(s) lacking enhancer activity, especially when present in an FV vector backbone that prevents read-through transcription. Although the pACT assay does not measure oncogenesis directly, it should be useful for screening vectors before more time-consuming and costly animal studies are undertaken.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • Blotting, Northern
  • Cell Line
  • Enhancer Elements, Genetic / genetics
  • Flow Cytometry
  • Gene Expression Regulation / genetics*
  • Genetic Vectors / genetics*
  • Green Fluorescent Proteins / genetics
  • Green Fluorescent Proteins / metabolism
  • HIV / genetics
  • Humans
  • K562 Cells
  • Leukemia Virus, Murine / genetics
  • Luciferases / genetics
  • Luciferases / metabolism
  • Models, Genetic
  • Promoter Regions, Genetic / genetics
  • Recombinant Fusion Proteins / genetics
  • Recombinant Fusion Proteins / metabolism
  • Simian foamy virus / genetics
  • Transcriptional Activation
  • Transfection

Substances

  • Recombinant Fusion Proteins
  • Green Fluorescent Proteins
  • Luciferases