ALS-causing SOD1 mutants generate vascular changes prior to motor neuron degeneration

Nat Neurosci. 2008 Apr;11(4):420-2. doi: 10.1038/nn2073. Epub 2008 Mar 16.

Abstract

We report here that amyotrophic lateral sclerosis-linked superoxide dismutase 1 (SOD1) mutants with different biochemical characteristics disrupted the blood-spinal cord barrier in mice by reducing the levels of the tight junction proteins ZO-1, occludin and claudin-5 between endothelial cells. This resulted in microhemorrhages with release of neurotoxic hemoglobin-derived products, reductions in microcirculation and hypoperfusion. SOD1 mutant-mediated endothelial damage accumulated before motor neuron degeneration and the neurovascular inflammatory response occurred, indicating that it was a central contributor to disease initiation.

Publication types

  • Comparative Study
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Amyotrophic Lateral Sclerosis / enzymology*
  • Amyotrophic Lateral Sclerosis / genetics
  • Amyotrophic Lateral Sclerosis / pathology
  • Animals
  • Blood-Brain Barrier / metabolism*
  • Blood-Brain Barrier / pathology
  • Capillaries / enzymology*
  • Capillaries / pathology
  • Claudin-5
  • Disease Progression
  • Endothelium, Vascular / metabolism*
  • Endothelium, Vascular / pathology
  • Hemorrhage / pathology
  • Humans
  • Isoenzymes / genetics
  • Isoenzymes / metabolism
  • Membrane Proteins / metabolism
  • Mice
  • Mice, Mutant Strains
  • Motor Neurons / pathology
  • Nerve Degeneration / metabolism
  • Occludin
  • Phosphoproteins / metabolism
  • Spinal Cord / blood supply
  • Spinal Cord / pathology
  • Superoxide Dismutase / genetics
  • Superoxide Dismutase / metabolism*
  • Superoxide Dismutase-1
  • Tight Junctions / enzymology
  • Tight Junctions / pathology
  • Zonula Occludens-1 Protein

Substances

  • Claudin-5
  • Cldn5 protein, mouse
  • Isoenzymes
  • Membrane Proteins
  • OCLN protein, human
  • Occludin
  • Ocln protein, mouse
  • Phosphoproteins
  • SOD1 protein, human
  • TJP1 protein, human
  • Tjp1 protein, mouse
  • Zonula Occludens-1 Protein
  • Sod1 protein, mouse
  • Superoxide Dismutase
  • Superoxide Dismutase-1