Lymphocyte gene therapy

Hum Gene Ther. 1991 Summer;2(2):107-9. doi: 10.1089/hum.1991.2.2-107.

Abstract

Genetically corrected T cells are currently under investigation as a treatment for severe combined immunodeficiency disease resulting from a lack of adenosine deaminase (ADA). Monthly injections of these ADA-corrected T cells have resulted in measurable ADA activity in the peripheral blood and the in vivo production of antibody to blood group antigen. Genetically corrected T cells appear to be clinically valuable vehicles for gene therapy.

Publication types

  • Clinical Trial

MeSH terms

  • Adenosine Deaminase / deficiency
  • Adenosine Deaminase / genetics*
  • Cells, Cultured
  • Child
  • Clinical Protocols
  • Genetic Therapy*
  • Humans
  • Severe Combined Immunodeficiency / enzymology
  • Severe Combined Immunodeficiency / genetics
  • Severe Combined Immunodeficiency / therapy*
  • T-Lymphocytes / enzymology*
  • T-Lymphocytes / transplantation
  • Transfection

Substances

  • Adenosine Deaminase