A large-scale mutation search reveals genetic heterogeneity in 3M syndrome

Eur J Hum Genet. 2009 Mar;17(3):395-400. doi: 10.1038/ejhg.2008.200. Epub 2008 Oct 29.

Abstract

The 3M syndrome is a rare autosomal recessive disorder recently ascribed to mutations in the CUL7 gene and characterized by severe pre- and postnatal growth retardation. Studying a series of 33 novel cases of 3M syndrome, we have identified deleterious CUL7 mutations in 23/33 patients, including 19 novel mutations and one paternal isodisomy of chromosome 6 encompassing a CUL7 mutation. Lack of mutations in 10/33 cases and exclusion of the CUL7 locus on chromosome 6p21.1 in six consanguineous families strongly support the genetic heterogeneity of the 3M syndrome.

MeSH terms

  • Abnormalities, Multiple / genetics*
  • Child
  • Child, Preschool
  • Consanguinity
  • Cullin Proteins / genetics*
  • Family
  • Fetal Growth Retardation / genetics
  • Fetus / diagnostic imaging
  • Fetus / pathology
  • Genes, Recessive
  • Genetic Heterogeneity*
  • Humans
  • Male
  • Mutation*
  • Radiography
  • Syndrome

Substances

  • CUL7 protein, human
  • Cullin Proteins