Potent and selective agonism of the melanocortin receptor 4 with MK-0493 does not induce weight loss in obese human subjects: energy intake predicts lack of weight loss efficacy

Clin Pharmacol Ther. 2009 Dec;86(6):659-66. doi: 10.1038/clpt.2009.167. Epub 2009 Sep 9.

Abstract

MK-0493 is a novel, potent, and selective agonist of the melanocortin receptor 4 (MC4R), one of the best-validated genetic targets and considered one of the most promising for the development of antiobesity therapeutics. An ad libitum energy-intake model was qualified with excellent reproducibility: the geometric mean ratio (GMR) with 95% confidence interval (CI) for total energy intake over a period of 24 h for 30 mg sibutramine/placebo was 0.82 (0.76, 0.88), and for 10 mg sibutramine/placebo it was 0.98 (0.91, 1.05). MK-0493 showed a small and marginally significant effect on 24-h energy intake, whereas 30 mg of sibutramine caused a significant reduction in total 24-h energy intake; specifically, the GMR (95% CI) for 30 mg sibutramine/placebo was 0.79 (0.74, 0.85). MK-0493 was associated with modest weight reduction from baseline but had only small, statistically insignificant effects relative to placebo after 12 weeks in a fixed-dose study and also after 18 weeks of stepped-titration dosing. We conclude that agonism of MC4R is not likely to represent a viable approach to the development of antiobesity therapeutics.

Trial registration: ClinicalTrials.gov NCT00482196.

Publication types

  • Clinical Trial, Phase I
  • Clinical Trial, Phase II
  • Comparative Study
  • Multicenter Study
  • Randomized Controlled Trial
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Acetamides / adverse effects
  • Acetamides / pharmacokinetics
  • Acetamides / therapeutic use*
  • Adult
  • Aged
  • Appetite / drug effects*
  • Appetite Depressants / adverse effects
  • Appetite Depressants / pharmacokinetics
  • Appetite Depressants / therapeutic use*
  • Cross-Over Studies
  • Cyclobutanes / therapeutic use*
  • Double-Blind Method
  • Energy Intake / drug effects*
  • England
  • Humans
  • Male
  • Middle Aged
  • Obesity / drug therapy*
  • Obesity / metabolism
  • Pyrrolidines / adverse effects
  • Pyrrolidines / pharmacokinetics
  • Pyrrolidines / therapeutic use*
  • Receptor, Melanocortin, Type 4 / agonists*
  • Receptor, Melanocortin, Type 4 / metabolism
  • Time Factors
  • Treatment Failure
  • United States
  • Weight Loss / drug effects*
  • Young Adult

Substances

  • Acetamides
  • Appetite Depressants
  • Cyclobutanes
  • MC4R protein, human
  • N-1-(2-(1-(tert-butyl-4-(2,4-difluorophenyl)pyrrolidin-3-yl)-5-chlorophenyl)ethyl)acetamide
  • Pyrrolidines
  • Receptor, Melanocortin, Type 4
  • sibutramine

Associated data

  • ClinicalTrials.gov/NCT00482196