A single mutation in human mitochondrial DNA polymerase Pol gammaA affects both polymerization and proofreading activities of only the holoenzyme

J Biol Chem. 2010 Sep 3;285(36):28105-16. doi: 10.1074/jbc.M110.122283. Epub 2010 May 31.

Abstract

Common causes of human mitochondrial diseases are mutations affecting DNA polymerase (Pol) gamma, the sole polymerase responsible for DNA synthesis in mitochondria. Although the polymerase and exonuclease active sites are located on the catalytic subunit Pol gammaA, in holoenzyme both activities are regulated by the accessory subunit Pol gammaB. Several patients with severe neurological and muscular disorders were reported to carry the Pol gammaA substitutions R232G or R232H, which lie outside of either active site. We report that Arg(232) substitutions have no effect on independent Pol gammaA activities but show major defects in the Pol gammaA-Pol gammaB holoenzyme, including decreased polymerase and increased exonuclease activities, the latter with decreased selectivity for mismatches. We show that Pol gammaB facilitates distinguishing mismatched from base-paired primer termini and that Pol gammaA Arg(232) is essential for mediating this regulatory function of the accessory subunit. This study provides a molecular basis for the disease symptoms exhibited by patients carrying those substitutions.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Amino Acid Substitution
  • Animals
  • Arginine
  • Base Pair Mismatch
  • Base Sequence
  • Catalytic Domain
  • Cell Line
  • DNA Polymerase gamma
  • DNA Repair
  • DNA, Mitochondrial / biosynthesis
  • DNA, Mitochondrial / genetics
  • DNA-Directed DNA Polymerase / chemistry*
  • DNA-Directed DNA Polymerase / genetics
  • DNA-Directed DNA Polymerase / metabolism*
  • Exodeoxyribonucleases / metabolism
  • Holoenzymes / chemistry
  • Holoenzymes / genetics
  • Holoenzymes / metabolism
  • Mitochondria / enzymology*
  • Mitochondria / metabolism
  • Models, Molecular
  • Mutation*
  • Protein Multimerization*
  • Protein Structure, Quaternary
  • Substrate Specificity

Substances

  • DNA, Mitochondrial
  • Holoenzymes
  • Arginine
  • DNA Polymerase gamma
  • DNA-Directed DNA Polymerase
  • Exodeoxyribonucleases