Durable hematological response and improvement of nephrotic syndrome on thalidomide therapy in a patient with refractory light chain deposition disease

Int J Hematol. 2011 May;93(5):673-676. doi: 10.1007/s12185-011-0829-4. Epub 2011 Apr 9.

Abstract

Light chain deposition disease (LCDD) is a rare disease for which an optimal treatment is not yet available. Here, we report the clinical course of a 32-year-old woman with LCDD who was successfully treated with thalidomide. She presented with nephrotic syndrome. Based on the renal biopsy findings and the presence of monoclonal immunoglobulin light chains in her serum and urine, LCDD was diagnosed. Prednisolone and cytotoxic chemotherapy used for multiple myeloma proved ineffective. We initiated administration of thalidomide (100 mg daily) and dexamethasone (20 mg for 4 days per month). After 8 months of treatment, she achieved complete hematological remission, defined as the disappearance of monoclonal protein and a normalized free light chain ratio, which led to improvement of her renal insufficiency. She has shown sustained hematological and organ response for 31 months with thalidomide therapy. Thus, thalidomide therapy seems to be a promising approach to the treatment of LCDD.

Publication types

  • Case Reports

MeSH terms

  • Adult
  • Dexamethasone / administration & dosage
  • Dexamethasone / therapeutic use
  • Drug Administration Schedule
  • Drug Therapy, Combination
  • Female
  • Humans
  • Immunoglobulin Light Chains / blood*
  • Immunoglobulin Light Chains / chemistry
  • Immunologic Factors / administration & dosage*
  • Immunologic Factors / therapeutic use
  • Kidney / metabolism*
  • Kidney / pathology
  • Multiple Myeloma / drug therapy
  • Nephrotic Syndrome / blood*
  • Nephrotic Syndrome / drug therapy*
  • Nephrotic Syndrome / pathology
  • Remission Induction / methods*
  • Thalidomide / administration & dosage*
  • Thalidomide / therapeutic use

Substances

  • Immunoglobulin Light Chains
  • Immunologic Factors
  • Thalidomide
  • Dexamethasone