IL-7 receptor expression identifies suicide gene-modified allospecific CD8+ T cells capable of self-renewal and differentiation into antileukemia effectors

Blood. 2011 Jun 16;117(24):6469-78. doi: 10.1182/blood-2010-11-320366. Epub 2011 Apr 29.

Abstract

In allogeneic hematopoietic cell transplantation (HSCT), donor T lymphocytes mediate the graft-versus-leukemia (GVL) effect, but induce graft-versus-host disease (GVHD). Suicide gene therapy-that is, the genetic induction of a conditional suicide phenotype into donor T cells-allows dissociating the GVL effect from GVHD. Genetic modification with retroviral vectors after CD3 activation reduces T-cell alloreactivity. We recently found that alloreactivity is maintained when CD28 costimulation, IL-7, and IL-15 are added. Herein, we used the minor histocompatibility (mH) antigens HA-1 and H-Y as model alloantigens to directly explore the antileukemia efficacy of human T cells modified with the prototypic suicide gene herpes simplex virus thymidine kinase (tk) after activation with different stimuli. Only in the case of CD28 costimulation, IL-7, and IL-15, the repertoire of tk(+) T cells contained HA-1- and H-Y-specific CD8(+) cytotoxic T cells (CTL) precursors. Thymidine kinase-positive HA-1- and H-Y-specific CTLs were capable of self-renewal and differentiation into potent antileukemia effectors in vitro, and in vivo in a humanized mouse model. Self-renewal and differentiation coincided with IL-7 receptor expression. These results pave the way to the clinical investigation of T cells modified with a suicide gene after CD28 costimulation, IL-7, and IL-15 for a safe and effective GVL effect.

Publication types

  • Evaluation Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Biomarkers / metabolism
  • CD8-Positive T-Lymphocytes / immunology*
  • CD8-Positive T-Lymphocytes / metabolism
  • Cell Differentiation* / genetics
  • Cell Differentiation* / immunology
  • Cell Proliferation*
  • Cells, Cultured
  • Female
  • Gene Expression / physiology
  • Genes, Transgenic, Suicide / immunology*
  • Genetic Therapy / methods
  • Genetic Vectors / immunology
  • Humans
  • Immunotherapy, Adoptive / methods
  • Leukemia / diagnosis*
  • Leukemia / genetics
  • Leukemia / immunology
  • Leukemia / therapy
  • Mice
  • Mice, Inbred NOD
  • Mice, SCID
  • Prognosis
  • Receptors, Interleukin-7 / genetics
  • Receptors, Interleukin-7 / metabolism
  • Receptors, Interleukin-7 / physiology*
  • T-Cell Antigen Receptor Specificity / genetics
  • T-Lymphocytes, Cytotoxic / immunology
  • T-Lymphocytes, Cytotoxic / metabolism
  • T-Lymphocytes, Cytotoxic / physiology
  • Transplantation, Homologous

Substances

  • Biomarkers
  • Receptors, Interleukin-7