Human kappa light chain targeted Pseudomonas exotoxin A--identifying human antibodies and Fab fragments with favorable characteristics for antibody-drug conjugate development

J Immunol Methods. 2011 Aug 31;371(1-2):122-33. doi: 10.1016/j.jim.2011.06.023. Epub 2011 Jun 30.

Abstract

Antibody-drug conjugates (ADC) represent promising agents for targeted cancer therapy. To allow rational selection of human antibodies with favorable characteristics for ADC development a screening tool was designed obviating the need of preparing individual covalently linked conjugates. Therefore, α-kappa-ETA' was designed as a fusion protein consisting of a human kappa light chain binding antibody fragment and a truncated version of Pseudomonas exotoxin A. α-kappa-ETA' specifically bound to human kappa light chains of human or human-mouse chimeric antibodies and Fab fragments. Antibody-redirected α-kappa-ETA' specifically inhibited proliferation of antigen-expressing cell lines at low toxin and antibody concentrations. Selected antibodies that efficiently delivered α-kappa-ETA' in the novel assay system were used to generate scFv-based covalently linked immunotoxins. These molecules efficiently triggered apoptosis of target cells, indicating that antibodies identified in our assay system can be converted to functional immunoconjugates. Finally, a panel of human epidermal growth factor receptor (EGFR) antibodies was screened--demonstrating favorable characteristics with antibody 2F8. These data suggest that antibodies with potential for Pseudomonas exotoxin A-based ADC development can be identified using the novel α-kappa-ETA' conjugate.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • ADP Ribose Transferases / immunology*
  • ADP Ribose Transferases / therapeutic use
  • Animals
  • Bacterial Toxins / immunology*
  • Bacterial Toxins / therapeutic use
  • Cell Line
  • Cytotoxicity, Immunologic
  • Enzyme-Linked Immunosorbent Assay
  • ErbB Receptors / immunology
  • Exotoxins / immunology*
  • Exotoxins / therapeutic use
  • Flow Cytometry
  • Humans
  • Immunoglobulin Fab Fragments / chemistry
  • Immunoglobulin Fab Fragments / isolation & purification
  • Immunoglobulin Fab Fragments / therapeutic use
  • Immunoglobulin kappa-Chains / chemistry
  • Immunoglobulin kappa-Chains / isolation & purification*
  • Immunoglobulin kappa-Chains / therapeutic use
  • Immunotoxins / chemistry
  • Immunotoxins / isolation & purification*
  • Immunotoxins / therapeutic use
  • Mice
  • Models, Molecular
  • Neoplasms / immunology
  • Neoplasms / therapy
  • Pseudomonas aeruginosa Exotoxin A
  • Recombinant Fusion Proteins / chemistry
  • Recombinant Fusion Proteins / immunology
  • Recombinant Fusion Proteins / isolation & purification
  • Recombinant Fusion Proteins / therapeutic use
  • Virulence Factors / immunology*
  • Virulence Factors / therapeutic use

Substances

  • Bacterial Toxins
  • Exotoxins
  • Immunoglobulin Fab Fragments
  • Immunoglobulin kappa-Chains
  • Immunotoxins
  • Recombinant Fusion Proteins
  • Virulence Factors
  • ADP Ribose Transferases
  • ErbB Receptors