A mouse model for spondyloepiphyseal dysplasia congenita with secondary osteoarthritis due to a Col2a1 mutation

J Bone Miner Res. 2012 Feb;27(2):413-28. doi: 10.1002/jbmr.547.

Abstract

Progeny of mice treated with the mutagen N-ethyl-N-nitrosourea (ENU) revealed a mouse, designated Longpockets (Lpk), with short humeri, abnormal vertebrae, and disorganized growth plates, features consistent with spondyloepiphyseal dysplasia congenita (SEDC). The Lpk phenotype was inherited as an autosomal dominant trait. Lpk/+ mice were viable and fertile and Lpk/Lpk mice died perinatally. Lpk was mapped to chromosome 15 and mutational analysis of likely candidates from the interval revealed a Col2a1 missense Ser1386Pro mutation. Transient transfection of wild-type and Ser1386Pro mutant Col2a1 c-Myc constructs in COS-7 cells and CH8 chondrocytes demonstrated abnormal processing and endoplasmic reticulum retention of the mutant protein. Histology revealed growth plate disorganization in 14-day-old Lpk/+ mice and embryonic cartilage from Lpk/+ and Lpk/Lpk mice had reduced safranin-O and type-II collagen staining in the extracellular matrix. The wild-type and Lpk/+ embryos had vertical columns of proliferating chondrocytes, whereas those in Lpk/Lpk mice were perpendicular to the direction of bone growth. Electron microscopy of cartilage from 18.5 dpc wild-type, Lpk/+, and Lpk/Lpk embryos revealed fewer and less elaborate collagen fibrils in the mutants, with enlarged vacuoles in the endoplasmic reticulum that contained amorphous inclusions. Micro-computed tomography (CT) scans of 12-week-old Lpk/+ mice revealed them to have decreased bone mineral density, and total bone volume, with erosions and osteophytes at the joints. Thus, an ENU mouse model with a Ser1386Pro mutation of the Col2a1 C-propeptide domain that results in abnormal collagen processing and phenotypic features consistent with SEDC and secondary osteoarthritis has been established.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Amino Acid Sequence
  • Animals
  • Base Sequence
  • Chondrocytes / metabolism
  • Chondrocytes / pathology
  • Chondrocytes / ultrastructure
  • Chromosomes, Mammalian / genetics
  • Collagen Type II / chemistry
  • Collagen Type II / genetics*
  • Disease Models, Animal
  • Embryo, Mammalian / abnormalities
  • Embryo, Mammalian / pathology
  • Genetic Loci / genetics
  • Growth Plate / abnormalities
  • Growth Plate / pathology
  • Male
  • Mice
  • Mice, Inbred C57BL
  • Molecular Sequence Data
  • Mutant Proteins / metabolism
  • Mutation, Missense / genetics*
  • Organ Size
  • Osteoarthritis / complications*
  • Osteoarthritis / genetics*
  • Osteochondrodysplasias / complications
  • Osteochondrodysplasias / congenital*
  • Osteochondrodysplasias / genetics
  • Osteogenesis
  • Phenotype
  • Physical Chromosome Mapping
  • Protein Processing, Post-Translational

Substances

  • Col2a1 protein, mouse
  • Collagen Type II
  • Mutant Proteins

Supplementary concepts

  • Spondyloepiphyseal dysplasia, congenita