Preliminary clinical activity of a topical JAK1/2 inhibitor in the treatment of psoriasis

J Am Acad Dermatol. 2012 Oct;67(4):658-64. doi: 10.1016/j.jaad.2011.12.018. Epub 2012 Jan 24.

Abstract

Background: Janus-associated kinases (JAKs) are involved in signal transduction from a variety of cytokines implicated in the pathogenesis of psoriasis, including interleukin (IL)-12, IL-23, and interferon-γ. INCB018424, a small molecule inhibitor of JAK1 and JAK2, inhibits cytokine-induced JAK/signal transducers and activators of transcription signaling and the resultant production of inflammatory proteins (eg, IL-17).

Objective: We sought to demonstrate proof of concept in patients with stable plaque psoriasis.

Methods: Patients were dosed with vehicle, 0.5% or 1.0% INCB018424 phosphate cream once a day or 1.5% twice a day for 28 days. Additional groups included two active comparators (calcipotriene 0.005% cream or betamethasone dipropionate 0.05% cream).

Results: Both the 1% and the 1.5% cream improved lesion thickness, erythema, and scaling and reduced lesion area compared with placebo. A composite lesion score decreased by greater than 50% with the efficacious doses of INCB018424 compared with 32% for vehicle controls. Topical application of INCB018424 was well tolerated with few mild adverse events noted. Mean plasma concentrations of INCB018424 after topical application of 0.5% to 1.5% cream were in the low nanomolar range, representing a fraction (<1%) of the half maximal inhibitory concentration (IC(50)) in whole blood for inhibition of cytokine-stimulated signal transducers and activators of transcription-3 phosphorylation.

Limitations: This study was limited by the relatively short study duration and small sample size.

Conclusion: Topical INCB018424 is safe, is well tolerated, and exhibits clinical activity in the topical treatment of psoriasis.

Trial registration: ClinicalTrials.gov NCT00820950.

Publication types

  • Comparative Study
  • Randomized Controlled Trial
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Aged
  • Anti-Inflammatory Agents / administration & dosage
  • Betamethasone / administration & dosage
  • Betamethasone / analogs & derivatives
  • Calcitriol / administration & dosage
  • Calcitriol / analogs & derivatives
  • Dermatologic Agents / administration & dosage
  • Enzyme Inhibitors / administration & dosage
  • Enzyme Inhibitors / adverse effects
  • Enzyme Inhibitors / pharmacokinetics
  • Female
  • Follow-Up Studies
  • Humans
  • Janus Kinase 1 / antagonists & inhibitors*
  • Janus Kinase 2 / antagonists & inhibitors*
  • Male
  • Middle Aged
  • Nitriles
  • Pilot Projects
  • Psoriasis / drug therapy*
  • Psoriasis / metabolism*
  • Pyrazoles / administration & dosage*
  • Pyrazoles / adverse effects
  • Pyrazoles / pharmacokinetics
  • Pyrimidines
  • Signal Transduction / drug effects
  • Signal Transduction / physiology
  • Treatment Outcome
  • Young Adult

Substances

  • Anti-Inflammatory Agents
  • Dermatologic Agents
  • Enzyme Inhibitors
  • Nitriles
  • Pyrazoles
  • Pyrimidines
  • calcipotriene
  • betamethasone-17,21-dipropionate
  • ruxolitinib
  • Betamethasone
  • JAK1 protein, human
  • JAK2 protein, human
  • Janus Kinase 1
  • Janus Kinase 2
  • Calcitriol

Associated data

  • ClinicalTrials.gov/NCT00820950