T-cell suicide gene therapy prompts thymic renewal in adults after hematopoietic stem cell transplantation

Blood. 2012 Aug 30;120(9):1820-30. doi: 10.1182/blood-2012-01-405670. Epub 2012 Jun 18.

Abstract

The genetic modification of T cells with a suicide gene grants a mechanism of control of adverse reactions, allowing safe infusion after partially incompatible hematopoietic stem cell transplantation (HSCT). In the TK007 clinical trial, 22 adults with hematologic malignancies experienced a rapid and sustained immune recovery after T cell-depleted HSCT and serial infusions of purified donor T cells expressing the HSV thymidine kinase suicide gene (TK+ cells). After a first wave of circulating TK+ cells, the majority of T cells supporting long-term immune reconstitution did not carry the suicide gene and displayed high numbers of naive lymphocytes, suggesting the thymus-dependent development of T cells, occurring only upon TK+ -cell engraftment. Accordingly, after the infusions, we documented an increase in circulating TCR excision circles and CD31+ recent thymic emigrants and a substantial expansion of the active thymic tissue as shown by chest tomography scans. Interestingly, a peak in the serum level of IL-7 was observed after each infusion of TK+ cells, anticipating the appearance of newly generated T cells. The results of the present study show that the infusion of genetically modified donor T cells after HSCT can drive the recovery of thymic activity in adults, leading to immune reconstitution.

Publication types

  • Clinical Trial, Phase I
  • Clinical Trial, Phase II
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Combined Modality Therapy
  • Gene Expression
  • Genes, Transgenic, Suicide / genetics
  • Genetic Therapy / methods*
  • Hematologic Neoplasms / blood
  • Hematologic Neoplasms / genetics
  • Hematologic Neoplasms / therapy*
  • Hematopoietic Stem Cell Transplantation / methods*
  • Humans
  • Interleukin-7 / blood
  • Lymphocyte Count
  • Prospective Studies
  • Radiography, Thoracic
  • Regeneration / genetics
  • Reverse Transcriptase Polymerase Chain Reaction
  • T-Lymphocytes / metabolism*
  • T-Lymphocytes / transplantation
  • Thymidine Kinase / genetics
  • Thymidine Kinase / metabolism
  • Thymus Gland / metabolism
  • Thymus Gland / physiopathology
  • Tomography, X-Ray Computed
  • Treatment Outcome

Substances

  • Interleukin-7
  • Thymidine Kinase