T-cell receptor gene transfer exclusively to human CD8(+) cells enhances tumor cell killing

Blood. 2012 Nov 22;120(22):4334-42. doi: 10.1182/blood-2012-02-412973. Epub 2012 Aug 16.

Abstract

Transfer of tumor-specific T-cell receptor (TCR) genes into patient T cells is a promising strategy in cancer immunotherapy. We describe here a novel vector (CD8-LV) derived from lentivirus, which delivers genes exclusively and specifically to CD8(+) cells. CD8-LV mediated stable in vitro and in vivo reporter gene transfer as well as efficient transfer of genes encoding TCRs recognizing the melanoma antigen tyrosinase. Strikingly, T cells genetically modified with CD8-LV killed melanoma cells reproducibly more efficiently than CD8(+) cells transduced with a conventional lentiviral vector. Neither TCR expression levels, nor the rate of activation-induced death of transduced cells differed between both vector types. Instead, CD8-LV transduced cells showed increased granzyme B and perforin levels as well as an up-regulation of CD8 surface expression in a small subpopulation of cells. Thus, a possible mechanism for CD8-LV enhanced tumor cell killing may be based on activation of the effector functions of CD8(+) T cells by the vector particle displaying OKT8-derived CD8-scFv and an increase of the surface density of CD8, which functions as coreceptor for tumor-cell recognition. CD8-LV represents a powerful novel vector for TCR gene therapy and other applications in immunotherapy and basic research requiring CD8(+) cell-specific gene delivery.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • CD8-Positive T-Lymphocytes / immunology
  • CD8-Positive T-Lymphocytes / metabolism*
  • CD8-Positive T-Lymphocytes / physiology
  • Cells, Cultured
  • Cytotoxicity, Immunologic / genetics*
  • Gene Transfer Techniques
  • Genetic Therapy / methods
  • HEK293 Cells
  • Humans
  • Immunotherapy, Adoptive / methods
  • Jurkat Cells
  • Mice
  • Mice, Inbred NOD
  • Mice, SCID
  • Models, Biological
  • Neoplasms / genetics
  • Neoplasms / immunology*
  • Organ Specificity / genetics
  • Receptors, Antigen, T-Cell / genetics*
  • Up-Regulation / genetics
  • Up-Regulation / immunology
  • Xenograft Model Antitumor Assays

Substances

  • Receptors, Antigen, T-Cell