Haploidentical transplantation in patients with acquired aplastic anemia

Bone Marrow Transplant. 2013 Feb;48(2):183-5. doi: 10.1038/bmt.2012.231. Epub 2013 Jan 7.

Abstract

Haploidentical SCT (haplo-SCT) has been considered a therapeutic option in patients with acquired severe aplastic anemia (SAA) failing at least one course of immune suppressive therapy with antithymocyte globulin and lacking an HLA-matched related or unrelated donor. The platforms of both ex vivo T-cell-depleted and unmanipulated grafts have been explored in children and adults. Overall, the primary objective of a stable haploidentical hematopoietic engraftment with a low rate of GVHD is unmet in a significant proportion of patients undergoing haplo-SCT for SAA. Haploidentical transplants for refractory SAA should be performed in a specialist center with major experience in hematopoietic SCT procedures and preferably performed within the framework of a local clinical protocol designed specifically to address the prevention of graft rejection and GVHD.

Publication types

  • Review

MeSH terms

  • Anemia, Aplastic / surgery*
  • Hematopoietic Stem Cell Transplantation / methods*
  • Humans