Practical and cost-effective measurement of B-domain deleted and full-length recombinant FVIII in the routine haemostasis laboratory

Haemophilia. 2013 May;19(3):e133-8. doi: 10.1111/hae.12093. Epub 2013 Feb 4.

Abstract

The assessment of recombinant FVIII (rFVIII) activity (FVIII:C) in plasma of patients is dependent on the assay. Notably, a calibration with a product-specific laboratory standard is recommended when measuring Refacto-AF(R) activity in plasma with a one-stage assay. The objective of this study was to facilitate the measurement of rFVIII, taking into account the recent demonstration that a calibration curve does not have to be included in each run. FVIII:C was measured in patients' samples after infusion of different types of rFVIII with a one-stage and a chromogenic assay calibrated either with pooled normal plasma or a product-specific laboratory standard. Results obtained with the one-stage coagulation assay were compared with these provided by a chromogenic assay. We confirmed that a calibration curve can be used for a prolonged period of time without loss of precision and accuracy. In such conditions, a stable relation between the calibration curves generated with a product-specific laboratory standard and plasma can be established. In patients' plasma, Refacto-AF levels measured with a one-stage FVIII assay calibrated with plasma or a product-specific laboratory standard diverged from -58% to -17% and from -25% to +18%, respectively, from the activity determined with a chromogenic substrate assay. By comparison, FVIII:C levels of full-length rFVIII measured with the one-stage assay calibrated with plasma were 6-49% lower than with the chromogenic assay. In a monocentric setting, the long-term stability of the calibration curves allows the implementation of a practical and cost-effective approach to determine rFVIII:C levels.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Calibration
  • Chromogenic Compounds / chemistry
  • Chromogenic Compounds / metabolism
  • Enzyme Assays* / standards
  • Factor VIII / analysis*
  • Factor VIII / biosynthesis
  • Factor VIII / standards
  • Hemophilia A / blood
  • Humans
  • Laboratories
  • Recombinant Proteins / analysis*
  • Recombinant Proteins / biosynthesis
  • Recombinant Proteins / standards
  • Reference Standards

Substances

  • Chromogenic Compounds
  • Recombinant Proteins
  • recombinant factor VIII SQ
  • F8 protein, human
  • Factor VIII