Dendritic cell-based immunotherapy in prevention and treatment of renal cell carcinoma: efficacy, safety, and activity of Ad-GM·CAIX in immunocompetent mouse models

J Immunother. 2013 Feb;36(2):102-11. doi: 10.1097/CJI.0b013e31827bec97.

Abstract

The dendritic cell vaccine DC-Ad-GM·CAIX is an active, specific immunotherapy with the potential of providing a safe and effective therapy against renal cell carcinoma (RCC). Using immunocompetent Balb/c mouse models we tested the efficacy and mechanism of the vaccine to prevent and treat the growth of a syngeneic RCC (RENCA) engineered to overexpress the human TAA carbonic anhydrase IX (NPR-IX). In a prevention model, NPR-IX tumor development was specifically and significantly delayed by 13 days in DC-Ad-GM·CAIX-treated mice (P < 0.001), tumor volumes were 79% smaller (day 24, P < 0.007), and body weight was maintained at study termination compared with the controls. Six of these mice remained tumor-free for > 1 year. In a treatment model, NPR-IX tumors remained smaller in DC-Ad-GM·CAIX-treated mice for 8 days (P < 0.002), achieving a 60% growth inhibition at termination. No vaccine-related organ toxicity was observed in either model. The critical mechanistic parameter separating responsive from nonresponsive tumors was hCAIX protein expression, demonstrated by aggressive growth of tumors that did not express hCAIX protein and in sham-treated mice (DC-Ad-Null). No murine serum anti-hCAIX antibodies were detected. Moreover, altered mechanisms of immunoediting as a means for immune evasion were suggested by differential gene expression (Ccl1, Hmgb1, Fgl2, Cd209a, and Klra2) and therapy evasion miRNAs (miR-1186, miR-98, miR-5097, miR-1942, and miR-708) in tumors that evaded DC-Ad-GM·CAIX immunotherapy. This is the first study in immunocompetent mice that provides a proof of concept for the specificity, efficacy, safety, and activity of the DC-Ad-GM·CAIX immunotherapy, forming the basis for a first-in-human phase I trial in RCC patients.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antibodies / blood
  • Cancer Vaccines / adverse effects
  • Cancer Vaccines / immunology
  • Cancer Vaccines / therapeutic use*
  • Carbonic Anhydrase IX
  • Carbonic Anhydrases / biosynthesis
  • Carbonic Anhydrases / immunology*
  • Carcinoma, Renal Cell / immunology
  • Carcinoma, Renal Cell / prevention & control*
  • Carcinoma, Renal Cell / therapy*
  • Cell Adhesion Molecules / biosynthesis
  • Cell Line, Tumor
  • Chemokine CCL1 / biosynthesis
  • Dendritic Cells / immunology*
  • Disease Models, Animal
  • Female
  • Fibrinogen / biosynthesis
  • Gene Expression
  • Immunotherapy, Adoptive*
  • Kidney Neoplasms / immunology
  • Kidney Neoplasms / prevention & control
  • Kidney Neoplasms / therapy*
  • Lectins, C-Type / biosynthesis
  • Mice
  • Mice, Inbred BALB C
  • MicroRNAs / genetics
  • NK Cell Lectin-Like Receptor Subfamily A / biosynthesis
  • Receptors, Cell Surface / biosynthesis

Substances

  • Antibodies
  • Cancer Vaccines
  • Ccl1 protein, mouse
  • Cell Adhesion Molecules
  • Chemokine CCL1
  • DC-specific ICAM-3 grabbing nonintegrin
  • Fgl2 protein, mouse
  • Klra2 protein, mouse
  • Lectins, C-Type
  • MicroRNAs
  • NK Cell Lectin-Like Receptor Subfamily A
  • Receptors, Cell Surface
  • Fibrinogen
  • Carbonic Anhydrase IX
  • Carbonic Anhydrases
  • Car9 protein, mouse