Mutations in the EXT1 and EXT2 genes in Spanish patients with multiple osteochondromas

Sci Rep. 2013:3:1346. doi: 10.1038/srep01346.

Abstract

Multiple osteochondromas is an autosomal dominant skeletal disorder characterized by the formation of multiple cartilage-capped tumours. Two causal genes have been identified, EXT1 and EXT2, which account for 65% and 30% of cases, respectively. We have undertaken a mutation analysis of the EXT1 and EXT2 genes in 39 unrelated Spanish patients, most of them with moderate phenotype, and looked for genotype-phenotype correlations. We found the mutant allele in 37 patients, 29 in EXT1 and 8 in EXT2. Five of the EXT1 mutations were deletions identified by MLPA. Two cases of mosaicism were documented. We detected a lower number of exostoses in patients with missense mutation versus other kinds of mutations. In conclusion, we found a mutation in EXT1 or in EXT2 in 95% of the Spanish patients. Eighteen of the mutations were novel.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Child
  • Exons
  • Exostoses, Multiple Hereditary / genetics*
  • Genetic Association Studies
  • Humans
  • Introns
  • Mutation Rate
  • Mutation*
  • N-Acetylglucosaminyltransferases / genetics*
  • Pedigree
  • Spain
  • White People / genetics*
  • Young Adult

Substances

  • N-Acetylglucosaminyltransferases
  • exostosin-1
  • exostosin-2