Assessing the potential cost-effectiveness of retesting IHC0, IHC1+, or FISH-negative early stage breast cancer patients for HER2 status

Cancer. 2013 Sep 1;119(17):3113-22. doi: 10.1002/cncr.28196. Epub 2013 Jun 17.

Abstract

Background: Fluorescence in situ hybridization (FISH) and immunohistochemistry (IHC) tests are commonly used to assess human epidermal growth factor 2 (HER2) status of tumors in patients with breast cancer. This analysis evaluates the likely cost-effectiveness of expanded retesting to assess HER2 tumor status in women with early stage breast cancer.

Methods: We developed a decision-analytic model to estimate the incremental cost-effectiveness ratio (ICER) of expanded reflex testing from a US payer perspective. Expanded reflex testing is defined as retesting tumor specimens from patients whose tumors are IHC0, IHC1+, or FISH-negative on their first test. In the base case, we assumed that 80% of patient tumors are initially IHC-tested and 20% are FISH-tested. Testing outcomes for IHC and FISH with and without retesting were based on published meta-analyses. The cost of tests and treatment and the long-term health outcomes were obtained from the literature.

Results: In the base case, we estimated that 2.27% of women who received expanded reflex testing would be HER2-positive and receive trastuzumab treatment: the projected ICER was $36,721 per life year or $39,745 per quality-adjusted life year (QALY). This varied between $47,100 per QALY and $35,500 per QALY if we assumed that 1%-8% of patients retested were then HER2+, respectively. The results of deterministic and probabilistic sensitivity analysis were robust. This strategy would result in 4700 (2000-17,000) patients being eligible to receive trastuzumab treatment annually.

Conclusions: Retesting patients who are IHC0, IHC1+, or FISH-negative is projected to be a cost-effective clinical strategy.

Keywords: HER2; HER2 testing; Herceptin; adjuvant; cost-effectiveness; cost-utility; early breast cancer; economics; pharmacoeconomics; trastuzumab.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Aged
  • Algorithms
  • Antibodies, Monoclonal, Humanized / therapeutic use
  • Antineoplastic Combined Chemotherapy Protocols / therapeutic use*
  • Biomarkers, Tumor / metabolism*
  • Breast Neoplasms / drug therapy*
  • Breast Neoplasms / economics*
  • Breast Neoplasms / metabolism
  • Breast Neoplasms / pathology
  • Cost-Benefit Analysis
  • Decision Support Techniques*
  • False Negative Reactions
  • Female
  • Health Care Costs
  • Humans
  • Immunohistochemistry / economics*
  • In Situ Hybridization, Fluorescence / economics*
  • Middle Aged
  • Neoplasm Staging
  • Patient Acceptance of Health Care
  • Quality-Adjusted Life Years
  • Receptor, ErbB-2 / metabolism*
  • Sensitivity and Specificity
  • Trastuzumab
  • United States

Substances

  • Antibodies, Monoclonal, Humanized
  • Biomarkers, Tumor
  • ERBB2 protein, human
  • Receptor, ErbB-2
  • Trastuzumab