Latency can be conferred to a variety of cytokines by fusion with latency-associated peptide from TGF-β

Expert Opin Drug Deliv. 2014 Jan;11(1):5-16. doi: 10.1517/17425247.2013.839655. Epub 2013 Sep 27.

Abstract

Objectives: Targeting cytokines to sites of disease has clear advantages because it increases their therapeutic index. We designed fusion proteins of the latent-associated peptide (LAP) derived from TGF-β with various cytokines via a matrix metalloproteinase (MMP) cleavage site. This design confers latency, increased half-life and targeting to sites of inflammation. The aim of this study is to determine whether this approach can be applied to cytokines of different molecular structures and sizes.

Methods: Mature cytokines cloned downstream of LAP and a MMP cleavage site were expressed in 293T cells and assessed for latency and biological activity by Western blotting and bioassay.

Results: We demonstrate here that fusion proteins of TGF-β, erythropoietin, IL-1ra, IL-10, IL-4, BMP-7, IGF1 and IL-17 were rendered latent by fusion to LAP, requiring cleavage to become active in respective bioassays. As further proof of principle, we also show that delivery of engineered TGF-β can inhibit experimental autoimmune encephalomyelitis and that this approach can be used to efficiently deliver cytokines to the brain and spinal cord in mice with this disease.

Conclusions: The latent cytokine approach can be successfully applied to a range of molecules, including cytokines of different molecular structure and mass, growth factors and a cytokine antagonist.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Cell Line
  • Cells, Cultured
  • Chick Embryo
  • Cytokines / genetics
  • Cytokines / metabolism*
  • Encephalomyelitis, Autoimmune, Experimental / drug therapy
  • Fibroblasts
  • HEK293 Cells
  • HeLa Cells
  • Humans
  • Insulin-Like Growth Factor I / genetics
  • Insulin-Like Growth Factor I / metabolism*
  • Matrix Metalloproteinase 1 / genetics
  • Matrix Metalloproteinase 1 / metabolism*
  • Mice
  • Mice, Inbred DBA
  • Mink
  • Molecular Targeted Therapy
  • Peptides / genetics
  • Peptides / metabolism*
  • Peptides / therapeutic use
  • Protein Precursors / genetics
  • Protein Precursors / metabolism*
  • Protein Precursors / therapeutic use
  • Recombinant Fusion Proteins / genetics
  • Recombinant Fusion Proteins / metabolism*
  • Recombinant Fusion Proteins / therapeutic use
  • Transforming Growth Factor beta / genetics
  • Transforming Growth Factor beta / metabolism*
  • Transforming Growth Factor beta / therapeutic use

Substances

  • Cytokines
  • Peptides
  • Protein Precursors
  • Recombinant Fusion Proteins
  • Transforming Growth Factor beta
  • latency-associated propeptide, TGF-beta
  • Insulin-Like Growth Factor I
  • Matrix Metalloproteinase 1