Efficient in vivo gene delivery using modified Tat peptide with cationic lipids

Biotechnol Lett. 2014 Jul;36(7):1447-52. doi: 10.1007/s10529-014-1497-2. Epub 2014 Feb 27.

Abstract

A combination of modified HIV-1 Tat (mTat) peptide and cationic lipids, FuGENE HD (FH), dramatically enhanced transfection efficiency across a range of cell lines when compared to mTat or FH alone (Biomaterials 35:1705-1715 2014). The efficiency of this Tat peptide combination was significantly higher than many commercial non-viral vectors. In this present study, we tested the feasibility of this non-viral vector, mTat/FH, in vivo using plasmid DNA encoding a luciferase gene. The results of the in vivo studies showed that animals administered mTat/FH/DNA intramuscularly had significantly higher and longer luciferase expression (≈7 months) than those with mTat/DNA, FH/DNA, or DNA alone. Histological evaluation showed little immune response in the muscles, livers, and kidneys of mice administered with the mTat/FH. The combination of mTat with FH could significantly improve transfection efficiency, expanding the potential use of non-viral gene vectors in vivo.

MeSH terms

  • Animals
  • Genes, Reporter
  • Lipid Metabolism*
  • Luciferases / analysis
  • Luciferases / genetics
  • Mice
  • Plasmids / metabolism
  • Transfection / methods*
  • tat Gene Products, Human Immunodeficiency Virus / metabolism*

Substances

  • tat Gene Products, Human Immunodeficiency Virus
  • Luciferases