Diagnosis of suspected inherited platelet function disorders: results of a worldwide survey

J Thromb Haemost. 2014 Sep;12(9):1562-9. doi: 10.1111/jth.12650. Epub 2014 Jul 25.

Abstract

Background: Diagnosis of inherited platelet function disorders (IPFDs) is important for appropriate management and to improve epidemiologic and clinical knowledge. However, there remains a lack of consensus on the diagnostic approach.

Objectives: To gain knowledge on the current practices for the diagnosis of IPFD worldwide.

Methods: A 67-item questionnaire was distributed to the ISTH members and to the members of several national hemostasis and thrombosis societies.

Results: A total of 202 laboratories from 37 countries participated in the survey. The most frequent criterion to define patients with a suspected IPFD was a history of mucocutaneous bleeding and no acquired cause, but heterogeneity on the identification criteria was evident. Only 64.5% of respondents performed a direct clinical interview. On average, each laboratory studied 72 patients per year. The most commonly used laboratory equipment were the light-transmission aggregometer, the Platelet Function Analyzer-100, and the flow cytometer. Screening tests were platelet count, peripheral blood smear, light-transmission aggregometry, and Platelet Function Analyzer-100. Second-step tests were flow cytometry, molecular genetic analysis, and electron microscopy. Methodologies varied widely. In total, ~ 14,000 patients were investigated yearly and 60% turned out to not have a defect. Of the remaining 40%, only 8.7% received a diagnosis at a molecular level.

Conclusions: Many laboratories worldwide are involved in the diagnosis of IPFD. A large fraction of the patients studied remain without a diagnosis. A high variability in the diagnostic approaches is evident.

Keywords: blood platelet disorders; clinical laboratory techniques; platelet activation; platelet function tests; platelets.

MeSH terms

  • Blood Platelet Disorders / diagnosis*
  • Blood Platelets / cytology
  • Cardiology / standards
  • Clinical Laboratory Techniques
  • Flow Cytometry
  • Humans
  • International Cooperation
  • Microscopy, Electron
  • Platelet Activation
  • Platelet Aggregation*
  • Platelet Count
  • Platelet Function Tests / instrumentation*
  • Societies, Medical
  • Surveys and Questionnaires