Construction of stable packaging cell lines for clinical lentiviral vector production

Sci Rep. 2015 Mar 12:5:9021. doi: 10.1038/srep09021.

Abstract

Lentiviral vectors are useful experimental tools for stable gene delivery and have been used to treat human inherited genetic disorders and hematologic malignancies with promising results. Because some of the lentiviral vector components are cytotoxic, transient plasmid transfection has been used to produce the large batches needed for clinical trials. However, this method is costly, poorly reproducible and hard to scale up. Here we describe a general method for construction of stable packaging cell lines that continuously produce lentiviral vectors. This uses Cre recombinase-mediated cassette exchange to insert a codon-optimised HIV-1 Gag-Pol expression construct in a continuously expressed locus in 293FT cells. Subsequently Rev, envelope and vector genome expression cassettes are serially transfected. Vector titers in excess of 10(6) transducing units/ml can be harvested from the final producer clones, which can be increased to 10(8) TU/ml by concentration. This method will be of use to all basic and clinical investigators who wish to produce large batches of lentiviral vectors.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Gene Expression
  • Genetic Vectors / genetics*
  • HEK293 Cells*
  • HIV-1 / genetics
  • HIV-1 / metabolism
  • Homologous Recombination
  • Humans
  • Lentivirus / genetics*
  • Protein Precursors / genetics
  • Protein Precursors / metabolism
  • Retroviridae / genetics
  • Retroviridae / metabolism
  • Viral Envelope Proteins / genetics
  • Viral Envelope Proteins / metabolism
  • Virus Assembly*
  • gag Gene Products, Human Immunodeficiency Virus / genetics
  • gag Gene Products, Human Immunodeficiency Virus / metabolism
  • pol Gene Products, Human Immunodeficiency Virus / genetics
  • pol Gene Products, Human Immunodeficiency Virus / metabolism
  • rev Gene Products, Human Immunodeficiency Virus / genetics
  • rev Gene Products, Human Immunodeficiency Virus / metabolism

Substances

  • Protein Precursors
  • Viral Envelope Proteins
  • gag Gene Products, Human Immunodeficiency Virus
  • pol Gene Products, Human Immunodeficiency Virus
  • pr160 gag-pol precursor protein, Human immunodeficiency virus 1
  • rev Gene Products, Human Immunodeficiency Virus
  • rev protein, Human Immunodeficiency Virus-1