Economic Comparison of an Empirical Versus Diagnostic-Driven Strategy for Treating Invasive Fungal Disease in Immunocompromised Patients

Clin Ther. 2015 Jun 1;37(6):1317-1328.e2. doi: 10.1016/j.clinthera.2015.03.021. Epub 2015 Apr 17.

Abstract

Purpose: Patients with persistent or recurrent neutropenic fevers at risk of invasive fungal disease (IFD) are treated empirically with antifungal therapy (AFT). Early treatment using a diagnostic-driven (DD) strategy may reduce clinical and economic burdens. We compared costs and outcomes of both strategies from a UK perspective.

Methods: An empirical strategy with conventional amphotericin B deoxycholate (C-AmB), liposomal amphotericin B (L-AmB), or caspofungin was compared with a DD strategy (initiated based on positive ELISA results for galactomannan antigen) and/or positive results for Aspergillus species on polymerase chain reaction assay) using C-AmB, voriconazole, or L-AmB in a decision-analytic model. Rates of IFD incidence, overall mortality, and IFD-related mortality in adults expected to be neutropenic for ≥10 days were obtained. The empirical strategy was assumed to identify 30% of IFD and targeted AFT to improve survival by a hazard ratio of 0.589. AFT-specific adverse events were obtained from a summary of product characteristics. Resource use was obtained, and costs were estimated by using standard UK costing sources. All costs are presented in 2012 British pounds sterling.

Findings: Total costs were 32% lower for the DD strategy (£1561.29) versus the empirical strategy (£2301.93) due to a reduced incidence of adverse events and decreased use of AFT. Administration of AFT was reduced by 41% (DD strategy, 74 of 1000; empirical strategy, 125 of 1000), with similar survival rates.

Implications: This study suggests that a DD strategy is likely to be cost-saving versus empirical treatment for immunocompromised patients with persistent or recurrent neutropenic fevers.

Keywords: antifungal therapy; aspergillosis; cost benefit; fungal infection.

Publication types

  • Comparative Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Amphotericin B / economics
  • Amphotericin B / therapeutic use
  • Antifungal Agents / economics*
  • Antifungal Agents / therapeutic use
  • Aspergillosis / diagnosis
  • Aspergillosis / drug therapy*
  • Aspergillosis / economics*
  • Aspergillus / isolation & purification
  • Caspofungin
  • Cost Savings
  • Decision Trees
  • Deoxycholic Acid / economics
  • Deoxycholic Acid / therapeutic use
  • Drug Combinations
  • Echinocandins / economics
  • Echinocandins / therapeutic use
  • Febrile Neutropenia / microbiology
  • Galactose / analogs & derivatives
  • Health Care Costs*
  • Health Resources / economics
  • Health Resources / statistics & numerical data
  • Humans
  • Immunocompromised Host*
  • Lipopeptides
  • Mannans / analysis
  • Survival Rate
  • Voriconazole / economics
  • Voriconazole / therapeutic use

Substances

  • Antifungal Agents
  • Drug Combinations
  • Echinocandins
  • Lipopeptides
  • Mannans
  • liposomal amphotericin B
  • Deoxycholic Acid
  • galactomannan
  • Amphotericin B
  • amphotericin B, deoxycholate drug combination
  • Caspofungin
  • Voriconazole
  • Galactose