Antiobesity Effect of a Small Molecule Repressor of RORγ

Mol Pharmacol. 2015 Jul;88(1):48-56. doi: 10.1124/mol.114.097485. Epub 2015 Apr 22.

Abstract

The orphan nuclear receptor RORγ is a key regulator for T helper 17 (TH17) cell differentiation, which regulates metabolic and circadian rhythm genes in peripheral tissues. Previously, it was shown that the small molecule inverse agonist of RORγ SR1555 [1-(4-((4'-(1,1,1,3,3,3-hexafluoro-2-hydroxypropan-2-yl)-[1,1'-biphenyl]-4-yl)methyl)piperazin-1-yl) ethanone] suppressed TH17 differentiation and stimulated induced T regulatory (iTreg) cells. Here, we show that treatment of cultured pre-adipocyctes with SR1555 represses the expression of RORγ while leading to increased expression of FGF21 and adipoQ. Chronic administration of SR1555 to obese diabetic mice resulted in a modest reduction in food intake accompanied with significant reduction in fat mass, resulting in reduced body weight and improved insulin sensitivity. Analysis ex vivo of treated mice demonstrates that SR1555 induced expression of the thermogenic gene program in fat depots. Further studies in cultured cells showed that SR1555 inhibited activation of hormone-sensitive lipase and increased fatty acid oxidation. Combined, these results suggest that pharmacological repression of RORγ may represent a strategy for treatment of obesity by increasing thermogenesis and fatty acid oxidation, while inhibition of hormone-sensitive lipase activity results in a reduction of serum free fatty acids, leading to improved peripheral insulin sensitivity.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, N.I.H., Intramural

MeSH terms

  • 3T3-L1 Cells
  • Adipogenesis / drug effects
  • Adiponectin / metabolism
  • Animals
  • Anti-Obesity Agents / administration & dosage*
  • Anti-Obesity Agents / chemical synthesis
  • Anti-Obesity Agents / pharmacology
  • Biphenyl Compounds / administration & dosage*
  • Biphenyl Compounds / chemical synthesis
  • Biphenyl Compounds / pharmacology
  • Body Weight / drug effects
  • Cells, Cultured
  • Diet, High-Fat
  • Fibroblast Growth Factors / metabolism
  • Insulin / metabolism*
  • Male
  • Mice
  • Nuclear Receptor Subfamily 1, Group F, Member 3 / antagonists & inhibitors*
  • Nuclear Receptor Subfamily 1, Group F, Member 3 / metabolism
  • Obesity / chemically induced
  • Obesity / drug therapy*
  • Obesity / genetics
  • Obesity / metabolism
  • Piperazines / administration & dosage*
  • Piperazines / chemical synthesis
  • Piperazines / pharmacology

Substances

  • Adiponectin
  • Adipoq protein, mouse
  • Anti-Obesity Agents
  • Biphenyl Compounds
  • Insulin
  • Nuclear Receptor Subfamily 1, Group F, Member 3
  • Piperazines
  • Rorc protein, mouse
  • SR1555
  • fibroblast growth factor 21
  • Fibroblast Growth Factors