Developing stem cell therapies for juvenile and adult-onset Huntington's disease

Regen Med. 2015;10(5):623-46. doi: 10.2217/rme.15.25.

Abstract

Stem cell therapies have been explored as a new avenue for the treatment of neurologic disease and damage within the CNS in part due to their native ability to mimic repair mechanisms in the brain. Mesenchymal stem cells have been of particular clinical interest due to their ability to release beneficial neurotrophic factors and their ability to foster a neuroprotective microenviroment. While early stem cell transplantation therapies have been fraught with technical and political concerns as well as limited clinical benefits, mesenchymal stem cell therapies have been shown to be clinically beneficial and derivable from nonembryonic, adult sources. The focus of this review will be on emerging and extant stem cell therapies for juvenile and adult-onset Huntington's disease.

Keywords: Huntington's disease; regenerative medicine; stem cell; transplantation.

Publication types

  • Review

MeSH terms

  • Adult
  • Animals
  • Animals, Genetically Modified
  • Cell Differentiation
  • Cell Transplantation / methods
  • Central Nervous System / pathology
  • Child
  • Clinical Trials as Topic
  • Disease Progression
  • Embryonic Stem Cells / cytology
  • Humans
  • Huntington Disease / therapy*
  • Immune System
  • Mesenchymal Stem Cell Transplantation
  • Mesenchymal Stem Cells / metabolism
  • Nerve Growth Factors / chemistry
  • Neurons / metabolism
  • Neuroprotection
  • Stem Cell Transplantation*

Substances

  • Nerve Growth Factors