Identification of tissue-restricted bioreaction suitable for in vivo targeting by fluorescent substrate library-based enzyme discovery

J Am Chem Soc. 2015 Sep 30;137(38):12187-90. doi: 10.1021/jacs.5b05884. Epub 2015 Sep 18.

Abstract

Tissue-restricted bioreactions can be utilized to design chemical-biological tools and prodrugs. We have developed a fluorescent-substrate-library-based enzyme discovery approach to screen tissue extracts for enzymatic activities of interest. Assay-positive candidate proteins were identified by diced electrophoresis gel assay followed by peptide mass fingerprinting. We discovered that pyruvyl anilide is specifically hydrolyzed by carboxylesterase 2 (CES2), which is predominantly localized in the liver and kidney. We show that the pyruvyl targeting group/CES2 enzyme pair can be used to deliver the 7-amino-4-methylcoumarin fluorophore specifically to the liver and kidney in vivo. Our screening approach should be useful to find other masking group/enzyme pairs suitable for development of fluorescent substrates and prodrugs.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Anilides / chemistry
  • Anilides / metabolism*
  • Carboxylesterase / metabolism*
  • Coumarins / chemistry
  • Coumarins / metabolism*
  • Enzyme Activation
  • Fluorescence*
  • Humans
  • Kidney / enzymology
  • Kidney / metabolism
  • Liver / enzymology
  • Liver / metabolism
  • Substrate Specificity

Substances

  • Anilides
  • Coumarins
  • CES2 protein, human
  • Carboxylesterase
  • 7-amino-4-methylcoumarin