Cardiomyocytes from human pluripotent stem cells: From laboratory curiosity to industrial biomedical platform

Biochim Biophys Acta. 2016 Jul;1863(7 Pt B):1728-48. doi: 10.1016/j.bbamcr.2015.10.014. Epub 2015 Oct 31.

Abstract

Cardiomyocytes from human pluripotent stem cells (hPSCs-CMs) could revolutionise biomedicine. Global burden of heart failure will soon reach USD $90bn, while unexpected cardiotoxicity underlies 28% of drug withdrawals. Advances in hPSC isolation, Cas9/CRISPR genome engineering and hPSC-CM differentiation have improved patient care, progressed drugs to clinic and opened a new era in safety pharmacology. Nevertheless, predictive cardiotoxicity using hPSC-CMs contrasts from failure to almost total success. Since this likely relates to cell immaturity, efforts are underway to use biochemical and biophysical cues to improve many of the ~30 structural and functional properties of hPSC-CMs towards those seen in adult CMs. Other developments needed for widespread hPSC-CM utility include subtype specification, cost reduction of large scale differentiation and elimination of the phenotyping bottleneck. This review will consider these factors in the evolution of hPSC-CM technologies, as well as their integration into high content industrial platforms that assess structure, mitochondrial function, electrophysiology, calcium transients and contractility. This article is part of a Special Issue entitled: Cardiomyocyte Biology: Integration of Developmental and Environmental Cues in the Heart edited by Marcus Schaub and Hughes Abriel.

Keywords: Automated scalability; Calcium imaging; Cardiomyocytes; Cas9/CRISPR genome editing; Contractility; Disease modelling; Drug screening; Electrophysiology; Engineered heart tissue; High content platforms; Human embryonic stem cells; Human induced pluripotent stem cells; Maturation factors; Mitochondria; Muscular thin films.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Biomedical Research / methods*
  • Cardiovascular Agents / pharmacology*
  • Cardiovascular Agents / toxicity
  • Cell Differentiation
  • Cell Lineage*
  • Cell Proliferation
  • Cells, Cultured
  • Drug Discovery / methods*
  • Genotype
  • Heart Diseases / chemically induced
  • Heart Diseases / drug therapy*
  • Heart Diseases / metabolism
  • Heart Diseases / pathology
  • Heart Diseases / physiopathology
  • High-Throughput Screening Assays*
  • Humans
  • Induced Pluripotent Stem Cells / drug effects
  • Induced Pluripotent Stem Cells / metabolism
  • Induced Pluripotent Stem Cells / physiology*
  • Myocytes, Cardiac / drug effects
  • Myocytes, Cardiac / metabolism
  • Myocytes, Cardiac / physiology*
  • Phenotype
  • Risk Assessment
  • Toxicity Tests / methods*

Substances

  • Cardiovascular Agents