Whole-transcriptome gene expression profiling in an epidermolysis bullosa simplex Dowling-Meara model keratinocyte cell line uncovered novel, potential therapeutic targets and affected pathways

BMC Res Notes. 2015 Dec 15:8:785. doi: 10.1186/s13104-015-1783-7.

Abstract

Background: To be able to develop effective therapeutics for epidermolysis bullosa simplex (EBS), it is necessary to elucidate the molecular pathomechanisms that give rise to the disease's characteristic severe skin-blistering phenotype.

Results: Starting with a whole-transcriptome microarray analysis of an EBS Dowling-Meara model cell line (KEB7), we identified 207 genes showing differential expression relative to control keratinocytes. A complementary qRT-PCR study of 156 candidates confirmed 76.58 % of the selected genes to be significantly up-regulated or down-regulated (p-value <0.05) within biological replicates. Our hit list contains previously identified genes involved in epithelial cell proliferation, cell-substrate adhesion, and responses to diverse biological stimuli. In addition, we identified novel candidate genes and potential affected pathways not previously considered as relevant to EBS pathology.

Conclusions: Our results broaden our understanding of the molecular processes dysregulated in EBS.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Blotting, Western
  • Cell Line
  • Epidermolysis Bullosa Simplex / drug therapy
  • Epidermolysis Bullosa Simplex / genetics
  • Epidermolysis Bullosa Simplex / pathology
  • Gene Expression Profiling / methods*
  • Gene Ontology
  • Genetic Predisposition to Disease / genetics
  • Humans
  • Keratinocytes / drug effects
  • Keratinocytes / metabolism*
  • Molecular Targeted Therapy / methods
  • Mutation
  • Oligonucleotide Array Sequence Analysis
  • Reverse Transcriptase Polymerase Chain Reaction
  • Signal Transduction / drug effects
  • Signal Transduction / genetics*
  • Transcriptome / genetics*