Upfront plerixafor plus G-CSF versus cyclophosphamide plus G-CSF for stem cell mobilization in multiple myeloma: efficacy and cost analysis study

Bone Marrow Transplant. 2016 Apr;51(4):546-52. doi: 10.1038/bmt.2015.322. Epub 2016 Jan 4.

Abstract

Cyclophosphamide plus G-CSF (C+G-CSF) is one of the most widely used stem cell (SC) mobilization regimens for patients with multiple myeloma (MM). Plerixafor plus G-CSF (P+G-CSF) has demonstrated superior SC mobilization efficacy when compared with G-CSF alone and has been shown to rescue patients who fail mobilization with G-CSF or C+G-CSF. Despite the proven efficacy of P+G-CSF in upfront SC mobilization, its use has been limited, mostly due to concerns of high price of the drug. However, a comprehensive comparison of the efficacy and cost effectiveness of SC mobilization using C+G-CSF versus P+G-CSF is not available. In this study, we compared 111 patients receiving C+G-CSF to 112 patients receiving P+G-CSF. The use of P+G-CSF was associated with a higher success rate of SC collection defined as ⩾5 × 10(6) CD34+ cells/kg (94 versus 83%, P=0.013) and less toxicities. Thirteen patients in the C+G-CSF arm were hospitalized owing to complications while none in the P+G-CSF group. C+G-CSF was associated with higher financial burden as assessed using institutional-specific costs and charges (P<0.001) as well as using Medicare reimbursement rates (P=0.27). Higher rate of hospitalization, increased need for salvage mobilization, and increased G-CSF use account for these differences.

Publication types

  • Comparative Study
  • Research Support, N.I.H., Extramural

MeSH terms

  • Autografts
  • Benzylamines
  • Costs and Cost Analysis
  • Cyclams
  • Cyclophosphamide* / administration & dosage
  • Cyclophosphamide* / economics
  • Female
  • Granulocyte Colony-Stimulating Factor* / administration & dosage
  • Granulocyte Colony-Stimulating Factor* / economics
  • Hematopoietic Stem Cell Mobilization / economics*
  • Hematopoietic Stem Cell Transplantation / economics*
  • Heterocyclic Compounds* / administration & dosage
  • Heterocyclic Compounds* / economics
  • Humans
  • Male
  • Multiple Myeloma* / economics
  • Multiple Myeloma* / therapy

Substances

  • Benzylamines
  • Cyclams
  • Heterocyclic Compounds
  • Granulocyte Colony-Stimulating Factor
  • Cyclophosphamide
  • plerixafor