Ex Vivo Costimulatory Blockade to Generate Regulatory T Cells From Patients Awaiting Kidney Transplantation

Am J Transplant. 2016 Jul;16(7):2187-95. doi: 10.1111/ajt.13725. Epub 2016 Mar 11.

Abstract

Short-term outcomes of kidney transplantation have improved dramatically, but chronic rejection and regimen-related toxicity continue to compromise overall patient outcomes. Development of regulatory T cells (Tregs) as a means to decrease alloresponsiveness and limit the need for pharmacologic immunosuppression is an active area of preclinical and clinical investigation. Nevertheless, the immunomodulatory effects of end-stage renal disease on the efficacy of various strategies to generate and expand recipient Tregs for kidney transplantation are incompletely characterized. In this study, we show that Tregs can be successfully generated from either freshly isolated or previously cryopreserved uremic recipient (responder) and healthy donor (stimulator) peripheral blood mononuclear cells using the strategy of ex vivo costimulatory blockade with belatacept during mixed lymphocyte culture. Moreover, these Tregs maintain a CD3(+) CD4(+) CD25(+) CD127(lo) surface phenotype, high levels of intracellular FOXP3 and significant demethylation of the FOXP3 Treg-specific demethylation region on allorestimulation with donor stimulator cells. These data support evaluation of this simple, brief Treg production strategy in clinical trials of mismatched kidney transplantation.

Trial registration: ClinicalTrials.gov NCT02091232.

Keywords: basic (laboratory) research/science; cellular transplantation (non-islet); kidney transplantation/nephrology; kidney transplantation: living donor; organ transplantation in general; tolerance: costimulation blockade; tolerance: experimental; translational research/science.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Abatacept / immunology
  • Adult
  • Aged
  • Female
  • Follow-Up Studies
  • Forkhead Transcription Factors / immunology
  • Glomerular Filtration Rate
  • Humans
  • Interleukin-2 Receptor alpha Subunit / immunology
  • Isoantigens / immunology*
  • Kidney Failure, Chronic / surgery*
  • Kidney Function Tests
  • Kidney Transplantation*
  • Leukocytes, Mononuclear / immunology*
  • Male
  • Middle Aged
  • Prognosis
  • Risk Factors
  • T-Lymphocytes, Regulatory / immunology*
  • Transplantation Tolerance / immunology*
  • Watchful Waiting

Substances

  • Forkhead Transcription Factors
  • IL2RA protein, human
  • Interleukin-2 Receptor alpha Subunit
  • Isoantigens
  • Abatacept

Associated data

  • ClinicalTrials.gov/NCT02091232